Zhijian Wu, Hongyan Yang, Peter Colosi. Mol Ther 2010
Times Cited: 449
Times Cited: 449
Times Cited
Times Co-cited
Similarity
A programmable dual-RNA-guided DNA endonuclease in adaptive bacterial immunity.
Martin Jinek, Krzysztof Chylinski, Ines Fonfara, Michael Hauer, Jennifer A Doudna, Emmanuelle Charpentier. Science 2012
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Dan Wang, Phillip W L Tai, Guangping Gao. Nat Rev Drug Discov 2019
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RNA-guided human genome engineering via Cas9.
Prashant Mali, Luhan Yang, Kevin M Esvelt, John Aach, Marc Guell, James E DiCarlo, Julie E Norville, George M Church. Science 2013
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Programmable editing of a target base in genomic DNA without double-stranded DNA cleavage.
Alexis C Komor, Yongjoo B Kim, Michael S Packer, John A Zuris, David R Liu. Nature 2016
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Programmable base editing of A•T to G•C in genomic DNA without DNA cleavage.
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Cationic lipid-mediated delivery of proteins enables efficient protein-based genome editing in vitro and in vivo.
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In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy.
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Engineering adeno-associated virus vectors for gene therapy.
Chengwen Li, R Jude Samulski. Nat Rev Genet 2020
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Identification of preexisting adaptive immunity to Cas9 proteins in humans.
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CRISPR-mediated modular RNA-guided regulation of transcription in eukaryotes.
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Nanoparticle delivery of Cas9 ribonucleoprotein and donor DNA in vivo induces homology-directed DNA repair.
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High-fidelity CRISPR-Cas9 nucleases with no detectable genome-wide off-target effects.
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In vivo-directed evolution of a new adeno-associated virus for therapeutic outer retinal gene delivery from the vitreous.
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Cre-dependent selection yields AAV variants for widespread gene transfer to the adult brain.
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A Single Administration of CRISPR/Cas9 Lipid Nanoparticles Achieves Robust and Persistent In Vivo Genome Editing.
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CRISPR provides acquired resistance against viruses in prokaryotes.
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Crystal structure of Cas9 in complex with guide RNA and target DNA.
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Gene disruption by cell-penetrating peptide-mediated delivery of Cas9 protein and guide RNA.
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Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo.
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Rationally engineered Cas9 nucleases with improved specificity.
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A multifunctional AAV-CRISPR-Cas9 and its host response.
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Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response.
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Emerging Issues in AAV-Mediated In Vivo Gene Therapy.
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Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy.
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7
Co-cited is the co-citation frequency, indicating how many articles cite the article together with the query article. Similarity is the co-citation as percentage of the times cited of the query article or the article in the search results, whichever is the lowest. These numbers are calculated for the last 100 citations when articles are cited more than 100 times.