Vedell Louis Jeune, Jakob A Joergensen, Roger J Hajjar, Thomas Weber. Hum Gene Ther Methods 2013
Times Cited: 151
Times Cited: 151
Times Cited
Times Co-cited
Similarity
Prevalence of serum IgG and neutralizing factors against adeno-associated virus (AAV) types 1, 2, 5, 6, 8, and 9 in the healthy population: implications for gene therapy using AAV vectors.
Sylvie Boutin, Virginie Monteilhet, Philippe Veron, Christian Leborgne, Olivier Benveniste, Marie Françoise Montus, Carole Masurier. Hum Gene Ther 2010
Sylvie Boutin, Virginie Monteilhet, Philippe Veron, Christian Leborgne, Olivier Benveniste, Marie Françoise Montus, Carole Masurier. Hum Gene Ther 2010
39
Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response.
Catherine S Manno, Glenn F Pierce, Valder R Arruda, Bertil Glader, Margaret Ragni, John J Rasko, Margareth C Ozelo, Keith Hoots, Philip Blatt, Barbara Konkle,[...]. Nat Med 2006
Catherine S Manno, Glenn F Pierce, Valder R Arruda, Bertil Glader, Margaret Ragni, John J Rasko, Margareth C Ozelo, Keith Hoots, Philip Blatt, Barbara Konkle,[...]. Nat Med 2006
35
Adenovirus-associated virus vector-mediated gene transfer in hemophilia B.
Amit C Nathwani, Edward G D Tuddenham, Savita Rangarajan, Cecilia Rosales, Jenny McIntosh, David C Linch, Pratima Chowdary, Anne Riddell, Arnulfo Jaquilmac Pie, Chris Harrington,[...]. N Engl J Med 2011
Amit C Nathwani, Edward G D Tuddenham, Savita Rangarajan, Cecilia Rosales, Jenny McIntosh, David C Linch, Pratima Chowdary, Anne Riddell, Arnulfo Jaquilmac Pie, Chris Harrington,[...]. N Engl J Med 2011
30
Long-term safety and efficacy of factor IX gene therapy in hemophilia B.
Amit C Nathwani, Ulreke M Reiss, Edward G D Tuddenham, Cecilia Rosales, Pratima Chowdary, Jenny McIntosh, Marco Della Peruta, Elsa Lheriteau, Nishal Patel, Deepak Raj,[...]. N Engl J Med 2014
Amit C Nathwani, Ulreke M Reiss, Edward G D Tuddenham, Cecilia Rosales, Pratima Chowdary, Jenny McIntosh, Marco Della Peruta, Elsa Lheriteau, Nishal Patel, Deepak Raj,[...]. N Engl J Med 2014
27
Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy.
Jerry R Mendell, Samiah Al-Zaidy, Richard Shell, W Dave Arnold, Louise R Rodino-Klapac, Thomas W Prior, Linda Lowes, Lindsay Alfano, Katherine Berry, Kathleen Church,[...]. N Engl J Med 2017
Jerry R Mendell, Samiah Al-Zaidy, Richard Shell, W Dave Arnold, Louise R Rodino-Klapac, Thomas W Prior, Linda Lowes, Lindsay Alfano, Katherine Berry, Kathleen Church,[...]. N Engl J Med 2017
27
Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant.
Lindsey A George, Spencer K Sullivan, Adam Giermasz, John E J Rasko, Benjamin J Samelson-Jones, Jonathan Ducore, Adam Cuker, Lisa M Sullivan, Suvankar Majumdar, Jerome Teitel,[...]. N Engl J Med 2017
Lindsey A George, Spencer K Sullivan, Adam Giermasz, John E J Rasko, Benjamin J Samelson-Jones, Jonathan Ducore, Adam Cuker, Lisa M Sullivan, Suvankar Majumdar, Jerome Teitel,[...]. N Engl J Med 2017
22
AAV5-Factor VIII Gene Transfer in Severe Hemophilia A.
Savita Rangarajan, Liron Walsh, Will Lester, David Perry, Bella Madan, Michael Laffan, Hua Yu, Christian Vettermann, Glenn F Pierce, Wing Y Wong,[...]. N Engl J Med 2017
Savita Rangarajan, Liron Walsh, Will Lester, David Perry, Bella Madan, Michael Laffan, Hua Yu, Christian Vettermann, Glenn F Pierce, Wing Y Wong,[...]. N Engl J Med 2017
22
Worldwide epidemiology of neutralizing antibodies to adeno-associated viruses.
Roberto Calcedo, Luk H Vandenberghe, Guangping Gao, Jianping Lin, James M Wilson. J Infect Dis 2009
Roberto Calcedo, Luk H Vandenberghe, Guangping Gao, Jianping Lin, James M Wilson. J Infect Dis 2009
22
Immune responses to AAV vectors: overcoming barriers to successful gene therapy.
Federico Mingozzi, Katherine A High. Blood 2013
Federico Mingozzi, Katherine A High. Blood 2013
21
Severe Toxicity in Nonhuman Primates and Piglets Following High-Dose Intravenous Administration of an Adeno-Associated Virus Vector Expressing Human SMN.
Christian Hinderer, Nathan Katz, Elizabeth L Buza, Cecilia Dyer, Tamara Goode, Peter Bell, Laura K Richman, James M Wilson. Hum Gene Ther 2018
Christian Hinderer, Nathan Katz, Elizabeth L Buza, Cecilia Dyer, Tamara Goode, Peter Bell, Laura K Richman, James M Wilson. Hum Gene Ther 2018
20
Unraveling the Complex Story of Immune Responses to AAV Vectors Trial After Trial.
Céline Vandamme, Oumeya Adjali, Federico Mingozzi. Hum Gene Ther 2017
Céline Vandamme, Oumeya Adjali, Federico Mingozzi. Hum Gene Ther 2017
19
Overcoming preexisting humoral immunity to AAV using capsid decoys.
Federico Mingozzi, Xavier M Anguela, Giulia Pavani, Yifeng Chen, Robert J Davidson, Daniel J Hui, Mustafa Yazicioglu, Liron Elkouby, Christian J Hinderer, Armida Faella,[...]. Sci Transl Med 2013
Federico Mingozzi, Xavier M Anguela, Giulia Pavani, Yifeng Chen, Robert J Davidson, Daniel J Hui, Mustafa Yazicioglu, Liron Elkouby, Christian J Hinderer, Armida Faella,[...]. Sci Transl Med 2013
18
Adeno-associated virus vector as a platform for gene therapy delivery.
Dan Wang, Phillip W L Tai, Guangping Gao. Nat Rev Drug Discov 2019
Dan Wang, Phillip W L Tai, Guangping Gao. Nat Rev Drug Discov 2019
16
Adeno-associated virus antibody profiles in newborns, children, and adolescents.
Roberto Calcedo, Hiroki Morizono, Lili Wang, Robert McCarter, Jianping He, David Jones, Mark L Batshaw, James M Wilson. Clin Vaccine Immunol 2011
Roberto Calcedo, Hiroki Morizono, Lili Wang, Robert McCarter, Jianping He, David Jones, Mark L Batshaw, James M Wilson. Clin Vaccine Immunol 2011
15
Systemic AAV Micro-dystrophin Gene Therapy for Duchenne Muscular Dystrophy.
Dongsheng Duan. Mol Ther 2018
Dongsheng Duan. Mol Ther 2018
15
Clades of Adeno-associated viruses are widely disseminated in human tissues.
Guangping Gao, Luk H Vandenberghe, Mauricio R Alvira, You Lu, Roberto Calcedo, Xiangyang Zhou, James M Wilson. J Virol 2004
Guangping Gao, Luk H Vandenberghe, Mauricio R Alvira, You Lu, Roberto Calcedo, Xiangyang Zhou, James M Wilson. J Virol 2004
15
CD8(+) T-cell responses to adeno-associated virus capsid in humans.
Federico Mingozzi, Marcela V Maus, Daniel J Hui, Denise E Sabatino, Samuel L Murphy, John E J Rasko, Margaret V Ragni, Catherine S Manno, Jurg Sommer, Haiyan Jiang,[...]. Nat Med 2007
Federico Mingozzi, Marcela V Maus, Daniel J Hui, Denise E Sabatino, Samuel L Murphy, John E J Rasko, Margaret V Ragni, Catherine S Manno, Jurg Sommer, Haiyan Jiang,[...]. Nat Med 2007
15
Gene therapy with adeno-associated virus vector 5-human factor IX in adults with hemophilia B.
Wolfgang Miesbach, Karina Meijer, Michiel Coppens, Peter Kampmann, Robert Klamroth, Roger Schutgens, Marco Tangelder, Giancarlo Castaman, Joachim Schwäble, Halvard Bonig,[...]. Blood 2018
Wolfgang Miesbach, Karina Meijer, Michiel Coppens, Peter Kampmann, Robert Klamroth, Roger Schutgens, Marco Tangelder, Giancarlo Castaman, Joachim Schwäble, Halvard Bonig,[...]. Blood 2018
14
Antigen-selective modulation of AAV immunogenicity with tolerogenic rapamycin nanoparticles enables successful vector re-administration.
Amine Meliani, Florence Boisgerault, Romain Hardet, Solenne Marmier, Fanny Collaud, Giuseppe Ronzitti, Christian Leborgne, Helena Costa Verdera, Marcelo Simon Sola, Severine Charles,[...]. Nat Commun 2018
Amine Meliani, Florence Boisgerault, Romain Hardet, Solenne Marmier, Fanny Collaud, Giuseppe Ronzitti, Christian Leborgne, Helena Costa Verdera, Marcelo Simon Sola, Severine Charles,[...]. Nat Commun 2018
14
Human immunoglobulin inhibits liver transduction by AAV vectors at low AAV2 neutralizing titers in SCID mice.
Ciaran D Scallan, Haiyan Jiang, Tongyao Liu, Susannah Patarroyo-White, Jurg M Sommer, Shangzhen Zhou, Linda B Couto, Glenn F Pierce. Blood 2006
Ciaran D Scallan, Haiyan Jiang, Tongyao Liu, Susannah Patarroyo-White, Jurg M Sommer, Shangzhen Zhou, Linda B Couto, Glenn F Pierce. Blood 2006
13
Neutralizing antibodies against adeno-associated virus examined prospectively in pediatric patients with hemophilia.
C Li, N Narkbunnam, R J Samulski, A Asokan, G Hu, L J Jacobson, M J Manco-Johnson, P E Monahan. Gene Ther 2012
C Li, N Narkbunnam, R J Samulski, A Asokan, G Hu, L J Jacobson, M J Manco-Johnson, P E Monahan. Gene Ther 2012
13
Structure-guided evolution of antigenically distinct adeno-associated virus variants for immune evasion.
Longping Victor Tse, Kelli A Klinc, Victoria J Madigan, Ruth M Castellanos Rivera, Lindsey F Wells, L Patrick Havlik, J Kennon Smith, Mavis Agbandje-McKenna, Aravind Asokan. Proc Natl Acad Sci U S A 2017
Longping Victor Tse, Kelli A Klinc, Victoria J Madigan, Ruth M Castellanos Rivera, Lindsey F Wells, L Patrick Havlik, J Kennon Smith, Mavis Agbandje-McKenna, Aravind Asokan. Proc Natl Acad Sci U S A 2017
13
A 10 patient case report on the impact of plasmapheresis upon neutralizing factors against adeno-associated virus (AAV) types 1, 2, 6, and 8.
Virginie Monteilhet, Samir Saheb, Sylvie Boutin, Christian Leborgne, Philippe Veron, Marie-Françoise Montus, Philippe Moullier, Olivier Benveniste, Carole Masurier. Mol Ther 2011
Virginie Monteilhet, Samir Saheb, Sylvie Boutin, Christian Leborgne, Philippe Veron, Marie-Françoise Montus, Philippe Moullier, Olivier Benveniste, Carole Masurier. Mol Ther 2011
13
Emerging Issues in AAV-Mediated In Vivo Gene Therapy.
Pasqualina Colella, Giuseppe Ronzitti, Federico Mingozzi. Mol Ther Methods Clin Dev 2017
Pasqualina Colella, Giuseppe Ronzitti, Federico Mingozzi. Mol Ther Methods Clin Dev 2017
13
Influence of Pre-existing Anti-capsid Neutralizing and Binding Antibodies on AAV Vector Transduction.
Zachary Fitzpatrick, Christian Leborgne, Elena Barbon, Elisa Masat, Giuseppe Ronzitti, Laetitia van Wittenberghe, Alban Vignaud, Fanny Collaud, Séverine Charles, Marcelo Simon Sola,[...]. Mol Ther Methods Clin Dev 2018
Zachary Fitzpatrick, Christian Leborgne, Elena Barbon, Elisa Masat, Giuseppe Ronzitti, Laetitia van Wittenberghe, Alban Vignaud, Fanny Collaud, Séverine Charles, Marcelo Simon Sola,[...]. Mol Ther Methods Clin Dev 2018
15
Overcoming the Host Immune Response to Adeno-Associated Virus Gene Delivery Vectors: The Race Between Clearance, Tolerance, Neutralization, and Escape.
Federico Mingozzi, Katherine A High. Annu Rev Virol 2017
Federico Mingozzi, Katherine A High. Annu Rev Virol 2017
12
A programmable dual-RNA-guided DNA endonuclease in adaptive bacterial immunity.
Martin Jinek, Krzysztof Chylinski, Ines Fonfara, Michael Hauer, Jennifer A Doudna, Emmanuelle Charpentier. Science 2012
Martin Jinek, Krzysztof Chylinski, Ines Fonfara, Michael Hauer, Jennifer A Doudna, Emmanuelle Charpentier. Science 2012
12
Recurrent AAV2-related insertional mutagenesis in human hepatocellular carcinomas.
Jean-Charles Nault, Shalini Datta, Sandrine Imbeaud, Andrea Franconi, Maxime Mallet, Gabrielle Couchy, Eric Letouzé, Camilla Pilati, Benjamin Verret, Jean-Frédéric Blanc,[...]. Nat Genet 2015
Jean-Charles Nault, Shalini Datta, Sandrine Imbeaud, Andrea Franconi, Maxime Mallet, Gabrielle Couchy, Eric Letouzé, Camilla Pilati, Benjamin Verret, Jean-Frédéric Blanc,[...]. Nat Genet 2015
11
Effect of genome size on AAV vector packaging.
Zhijian Wu, Hongyan Yang, Peter Colosi. Mol Ther 2010
Zhijian Wu, Hongyan Yang, Peter Colosi. Mol Ther 2010
11
Bioengineered AAV Capsids with Combined High Human Liver Transduction In Vivo and Unique Humoral Seroreactivity.
Nicole K Paulk, Katja Pekrun, Erhua Zhu, Sean Nygaard, Bin Li, Jianpeng Xu, Kirk Chu, Christian Leborgne, Allison P Dane, Annelise Haft,[...]. Mol Ther 2018
Nicole K Paulk, Katja Pekrun, Erhua Zhu, Sean Nygaard, Bin Li, Jianpeng Xu, Kirk Chu, Christian Leborgne, Allison P Dane, Annelise Haft,[...]. Mol Ther 2018
11
Selection and evaluation of clinically relevant AAV variants in a xenograft liver model.
Leszek Lisowski, Allison P Dane, Kirk Chu, Yue Zhang, Sharon C Cunningham, Elizabeth M Wilson, Sean Nygaard, Markus Grompe, Ian E Alexander, Mark A Kay. Nature 2014
Leszek Lisowski, Allison P Dane, Kirk Chu, Yue Zhang, Sharon C Cunningham, Elizabeth M Wilson, Sean Nygaard, Markus Grompe, Ian E Alexander, Mark A Kay. Nature 2014
11
Effects of transient immunosuppression on adenoassociated, virus-mediated, liver-directed gene transfer in rhesus macaques and implications for human gene therapy.
Haiyan Jiang, Linda B Couto, Susannah Patarroyo-White, Tongyao Liu, Dea Nagy, Joseph A Vargas, Shangzhen Zhou, Ciaran D Scallan, Jurg Sommer, Sharmila Vijay,[...]. Blood 2006
Haiyan Jiang, Linda B Couto, Susannah Patarroyo-White, Tongyao Liu, Dea Nagy, Joseph A Vargas, Shangzhen Zhou, Ciaran D Scallan, Jurg Sommer, Sharmila Vijay,[...]. Blood 2006
11
In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy.
Christopher E Nelson, Chady H Hakim, David G Ousterout, Pratiksha I Thakore, Eirik A Moreb, Ruth M Castellanos Rivera, Sarina Madhavan, Xiufang Pan, F Ann Ran, Winston X Yan,[...]. Science 2016
Christopher E Nelson, Chady H Hakim, David G Ousterout, Pratiksha I Thakore, Eirik A Moreb, Ruth M Castellanos Rivera, Sarina Madhavan, Xiufang Pan, F Ann Ran, Winston X Yan,[...]. Science 2016
11
The TLR9-MyD88 pathway is critical for adaptive immune responses to adeno-associated virus gene therapy vectors in mice.
Jiangao Zhu, Xiaopei Huang, Yiping Yang. J Clin Invest 2009
Jiangao Zhu, Xiaopei Huang, Yiping Yang. J Clin Invest 2009
11
Plasmapheresis eliminates the negative impact of AAV antibodies on microdystrophin gene expression following vascular delivery.
L G Chicoine, C L Montgomery, W G Bremer, K M Shontz, D A Griffin, K N Heller, S Lewis, V Malik, W E Grose, C J Shilling,[...]. Mol Ther 2014
L G Chicoine, C L Montgomery, W G Bremer, K M Shontz, D A Griffin, K N Heller, S Lewis, V Malik, W E Grose, C J Shilling,[...]. Mol Ther 2014
12
Adeno-Associated Virus (AAV) as a Vector for Gene Therapy.
Michael F Naso, Brian Tomkowicz, William L Perry, William R Strohl. BioDrugs 2017
Michael F Naso, Brian Tomkowicz, William L Perry, William R Strohl. BioDrugs 2017
11
Directed evolution of adeno-associated virus yields enhanced gene delivery vectors.
Narendra Maheshri, James T Koerber, Brian K Kaspar, David V Schaffer. Nat Biotechnol 2006
Narendra Maheshri, James T Koerber, Brian K Kaspar, David V Schaffer. Nat Biotechnol 2006
11
Analysis of AAV serotypes 1-9 mediated gene expression and tropism in mice after systemic injection.
Carmela Zincarelli, Stephen Soltys, Giuseppe Rengo, Joseph E Rabinowitz. Mol Ther 2008
Carmela Zincarelli, Stephen Soltys, Giuseppe Rengo, Joseph E Rabinowitz. Mol Ther 2008
11
Engineering adeno-associated virus vectors for gene therapy.
Chengwen Li, R Jude Samulski. Nat Rev Genet 2020
Chengwen Li, R Jude Samulski. Nat Rev Genet 2020
11
IgG-cleaving endopeptidase enables in vivo gene therapy in the presence of anti-AAV neutralizing antibodies.
Christian Leborgne, Elena Barbon, Jeffrey M Alexander, Hayley Hanby, Sandrine Delignat, Daniel M Cohen, Fanny Collaud, Saghana Muraleetharan, Dan Lupo, Joseph Silverberg,[...]. Nat Med 2020
Christian Leborgne, Elena Barbon, Jeffrey M Alexander, Hayley Hanby, Sandrine Delignat, Daniel M Cohen, Fanny Collaud, Saghana Muraleetharan, Dan Lupo, Joseph Silverberg,[...]. Nat Med 2020
12
Strategy to detect pre-existing immunity to AAV gene therapy.
L Falese, K Sandza, B Yates, S Triffault, S Gangar, B Long, L Tsuruda, B Carter, C Vettermann, S J Zoog,[...]. Gene Ther 2017
L Falese, K Sandza, B Yates, S Triffault, S Gangar, B Long, L Tsuruda, B Carter, C Vettermann, S J Zoog,[...]. Gene Ther 2017
23
Neutralizing antibodies against AAV2, AAV5 and AAV8 in healthy and HIV-1-infected subjects in China: implications for gene therapy using AAV vectors.
Q Liu, W Huang, H Zhang, Y Wang, J Zhao, A Song, H Xie, C Zhao, D Gao, Y Wang. Gene Ther 2014
Q Liu, W Huang, H Zhang, Y Wang, J Zhao, A Song, H Xie, C Zhao, D Gao, Y Wang. Gene Ther 2014
21
Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy.
Guang-Ping Gao, Mauricio R Alvira, Lili Wang, Roberto Calcedo, Julie Johnston, James M Wilson. Proc Natl Acad Sci U S A 2002
Guang-Ping Gao, Mauricio R Alvira, Lili Wang, Roberto Calcedo, Julie Johnston, James M Wilson. Proc Natl Acad Sci U S A 2002
10
In vitro and in vivo gene therapy vector evolution via multispecies interbreeding and retargeting of adeno-associated viruses.
Dirk Grimm, Joyce S Lee, Lora Wang, Tushar Desai, Bassel Akache, Theresa A Storm, Mark A Kay. J Virol 2008
Dirk Grimm, Joyce S Lee, Lora Wang, Tushar Desai, Bassel Akache, Theresa A Storm, Mark A Kay. J Virol 2008
10
Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes.
Kevin D Foust, Emily Nurre, Chrystal L Montgomery, Anna Hernandez, Curtis M Chan, Brian K Kaspar. Nat Biotechnol 2009
Kevin D Foust, Emily Nurre, Chrystal L Montgomery, Anna Hernandez, Curtis M Chan, Brian K Kaspar. Nat Biotechnol 2009
10
Prevalence of Anti-Adeno-Associated Virus Immune Responses in International Cohorts of Healthy Donors.
Anita Kruzik, Damir Fetahagic, Bettina Hartlieb, Sebastian Dorn, Herwig Koppensteiner, Frank M Horling, Friedrich Scheiflinger, Birgit M Reipert, Maurus de la Rosa. Mol Ther Methods Clin Dev 2019
Anita Kruzik, Damir Fetahagic, Bettina Hartlieb, Sebastian Dorn, Herwig Koppensteiner, Frank M Horling, Friedrich Scheiflinger, Birgit M Reipert, Maurus de la Rosa. Mol Ther Methods Clin Dev 2019
20
Basic biology of adeno-associated virus (AAV) vectors used in gene therapy.
Balaji Balakrishnan, Giridhara R Jayandharan. Curr Gene Ther 2014
Balaji Balakrishnan, Giridhara R Jayandharan. Curr Gene Ther 2014
10
Engineering adeno-associated viruses for clinical gene therapy.
Melissa A Kotterman, David V Schaffer. Nat Rev Genet 2014
Melissa A Kotterman, David V Schaffer. Nat Rev Genet 2014
9
Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial.
Stephen Russell, Jean Bennett, Jennifer A Wellman, Daniel C Chung, Zi-Fan Yu, Amy Tillman, Janet Wittes, Julie Pappas, Okan Elci, Sarah McCague,[...]. Lancet 2017
Stephen Russell, Jean Bennett, Jennifer A Wellman, Daniel C Chung, Zi-Fan Yu, Amy Tillman, Janet Wittes, Julie Pappas, Okan Elci, Sarah McCague,[...]. Lancet 2017
9
Cre-dependent selection yields AAV variants for widespread gene transfer to the adult brain.
Benjamin E Deverman, Piers L Pravdo, Bryan P Simpson, Sripriya Ravindra Kumar, Ken Y Chan, Abhik Banerjee, Wei-Li Wu, Bin Yang, Nina Huber, Sergiu P Pasca,[...]. Nat Biotechnol 2016
Benjamin E Deverman, Piers L Pravdo, Bryan P Simpson, Sripriya Ravindra Kumar, Ken Y Chan, Abhik Banerjee, Wei-Li Wu, Bin Yang, Nina Huber, Sergiu P Pasca,[...]. Nat Biotechnol 2016
9
Co-cited is the co-citation frequency, indicating how many articles cite the article together with the query article. Similarity is the co-citation as percentage of the times cited of the query article or the article in the search results, whichever is the lowest. These numbers are calculated for the last 100 citations when articles are cited more than 100 times.