A citation-based method for searching scientific literature

Maria Sessa, Laura Lorioli, Francesca Fumagalli, Serena Acquati, Daniela Redaelli, Cristina Baldoli, Sabrina Canale, Ignazio D Lopez, Francesco Morena, Andrea Calabria, Rossana Fiori, Paolo Silvani, Paola M V Rancoita, Michela Gabaldo, Fabrizio Benedicenti, Gigliola Antonioli, Andrea Assanelli, Maria Pia Cicalese, Ubaldo Del Carro, Maria Grazia Natali Sora, Sabata Martino, Angelo Quattrini, Eugenio Montini, Clelia Di Serio, Fabio Ciceri, Maria Grazia Roncarolo, Alessandro Aiuti, Luigi Naldini, Alessandra Biffi. Lancet 2016
Times Cited: 281







List of co-cited articles
1261 articles co-cited >1



Times Cited
  Times     Co-cited
Similarity


Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy.
Alessandra Biffi, Eugenio Montini, Laura Lorioli, Martina Cesani, Francesca Fumagalli, Tiziana Plati, Cristina Baldoli, Sabata Martino, Andrea Calabria, Sabrina Canale,[...]. Science 2013
793
55

Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy.
Florian Eichler, Christine Duncan, Patricia L Musolino, Paul J Orchard, Satiro De Oliveira, Adrian J Thrasher, Myriam Armant, Colleen Dansereau, Troy C Lund, Weston P Miller,[...]. N Engl J Med 2017
265
34

Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy.
Nathalie Cartier, Salima Hacein-Bey-Abina, Cynthia C Bartholomae, Gabor Veres, Manfred Schmidt, Ina Kutschera, Michel Vidaud, Ulrich Abel, Liliane Dal-Cortivo, Laure Caccavelli,[...]. Science 2009
29

Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome.
Alessandro Aiuti, Luca Biasco, Samantha Scaramuzza, Francesca Ferrua, Maria Pia Cicalese, Cristina Baricordi, Francesca Dionisio, Andrea Calabria, Stefania Giannelli, Maria Carmina Castiello,[...]. Science 2013
722
26

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia.
Marina Cavazzana-Calvo, Emmanuel Payen, Olivier Negre, Gary Wang, Kathleen Hehir, Floriane Fusil, Julian Down, Maria Denaro, Troy Brady, Karen Westerman,[...]. Nature 2010
883
22

Long-term Outcome of Allogeneic Hematopoietic Stem Cell Transplantation in Patients With Juvenile Metachromatic Leukodystrophy Compared With Nontransplanted Control Patients.
Samuel Groeschel, Jörn-Sven Kühl, Annette E Bley, Christiane Kehrer, Bernhard Weschke, Michaela Döring, Judith Böhringer, Johanna Schrum, René Santer, Alfried Kohlschütter,[...]. JAMA Neurol 2016
59
28

Long-term outcomes after allogeneic hematopoietic stem cell transplantation for metachromatic leukodystrophy: the largest single-institution cohort report.
Alexander A Boucher, Weston Miller, Ryan Shanley, Richard Ziegler, Troy Lund, Gerald Raymond, Paul J Orchard. Orphanet J Rare Dis 2015
80
21

Gene therapy of metachromatic leukodystrophy reverses neurological damage and deficits in mice.
Alessandra Biffi, Alessia Capotondo, Stefania Fasano, Ubaldo del Carro, Sergio Marchesini, Hisaya Azuma, Maria Chiara Malaguti, Stefano Amadio, Riccardo Brambilla, Markus Grompe,[...]. J Clin Invest 2006
160
17

Gene therapy augments the efficacy of hematopoietic cell transplantation and fully corrects mucopolysaccharidosis type I phenotype in the mouse model.
Ilaria Visigalli, Stefania Delai, Letterio S Politi, Carmela Di Domenico, Federica Cerri, Emanuela Mrak, Raffaele D'Isa, Daniela Ungaro, Merel Stok, Francesca Sanvito,[...]. Blood 2010
129
16

Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study.
Francesca Ferrua, Maria Pia Cicalese, Stefania Galimberti, Stefania Giannelli, Francesca Dionisio, Federica Barzaghi, Maddalena Migliavacca, Maria Ester Bernardo, Valeria Calbi, Andrea Angelo Assanelli,[...]. Lancet Haematol 2019
96
15

Brain conditioning is instrumental for successful microglia reconstitution following hematopoietic stem cell transplantation.
Alessia Capotondo, Rita Milazzo, Letterio Salvatore Politi, Angelo Quattrini, Alessio Palini, Tiziana Plati, Stefania Merella, Alessandro Nonis, Clelia di Serio, Eugenio Montini,[...]. Proc Natl Acad Sci U S A 2012
122
15

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia.
Sarah Marktel, Samantha Scaramuzza, Maria Pia Cicalese, Fabio Giglio, Stefania Galimberti, Maria Rosa Lidonnici, Valeria Calbi, Andrea Assanelli, Maria Ester Bernardo, Claudia Rossi,[...]. Nat Med 2019
122
14

LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1.
S Hacein-Bey-Abina, C Von Kalle, M Schmidt, M P McCormack, N Wulffraat, P Leboulch, A Lim, C S Osborne, R Pawliuk, E Morillon,[...]. Science 2003
14

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia.
Alexis A Thompson, Mark C Walters, Janet Kwiatkowski, John E J Rasko, Jean-Antoine Ribeil, Suradej Hongeng, Elisa Magrin, Gary J Schiller, Emmanuel Payen, Michaela Semeraro,[...]. N Engl J Med 2018
336
14

Brain-targeted stem cell gene therapy corrects mucopolysaccharidosis type II via multiple mechanisms.
Hélène Fe Gleitz, Ai Yin Liao, James R Cook, Samuel F Rowlston, Gabriella Ma Forte, Zelpha D'Souza, Claire O'Leary, Rebecca J Holley, Brian W Bigger. EMBO Mol Med 2018
42
30

Metachromatic leukodystrophy: Disease spectrum and approaches for treatment.
Diane F van Rappard, Jaap Jan Boelens, Nicole I Wolf. Best Pract Res Clin Endocrinol Metab 2015
83
15

Safety of intrathecal delivery of recombinant human arylsulfatase A in children with metachromatic leukodystrophy: Results from a phase 1/2 clinical trial.
Christine Í Dali, Caroline Sevin, Ingeborg Krägeloh-Mann, Roberto Giugliani, Norio Sakai, James Wu, Margaret Wasilewski. Mol Genet Metab 2020
25
52

Gene therapy using haematopoietic stem and progenitor cells.
Giuliana Ferrari, Adrian J Thrasher, Alessandro Aiuti. Nat Rev Genet 2021
60
21

Self-inactivating lentivirus vector for safe and efficient in vivo gene delivery.
R Zufferey, T Dull, R J Mandel, A Bukovsky, D Quiroz, L Naldini, D Trono. J Virol 1998
12

Lentiviral gene therapy for X-linked chronic granulomatous disease.
Donald B Kohn, Claire Booth, Elizabeth M Kang, Sung-Yun Pai, Kit L Shaw, Giorgia Santilli, Myriam Armant, Karen F Buckland, Uimook Choi, Suk See De Ravin,[...]. Nat Med 2020
92
13

Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy.
Jerry R Mendell, Samiah Al-Zaidy, Richard Shell, W Dave Arnold, Louise R Rodino-Klapac, Thomas W Prior, Linda Lowes, Lindsay Alfano, Katherine Berry, Kathleen Church,[...]. N Engl J Med 2017
12

Intracerebral administration of adeno-associated viral vector serotype rh.10 carrying human SGSH and SUMF1 cDNAs in children with mucopolysaccharidosis type IIIA disease: results of a phase I/II trial.
Marc Tardieu, Michel Zérah, Béatrice Husson, Stéphanie de Bournonville, Kumaran Deiva, Catherine Adamsbaum, Fanny Vincent, Michael Hocquemiller, Christine Broissand, Valérie Furlan,[...]. Hum Gene Ther 2014
163
11

Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients.
Steven J Howe, Marc R Mansour, Kerstin Schwarzwaelder, Cynthia Bartholomae, Michael Hubank, Helena Kempski, Martijn H Brugman, Karin Pike-Overzet, Stephen J Chatters, Dick de Ridder,[...]. J Clin Invest 2008
828
11

Gene therapy for Wiskott-Aldrich syndrome--long-term efficacy and genotoxicity.
Christian Jörg Braun, Kaan Boztug, Anna Paruzynski, Maximilian Witzel, Adrian Schwarzer, Michael Rothe, Ute Modlich, Rita Beier, Gudrun Göhring, Doris Steinemann,[...]. Sci Transl Med 2014
337
11

Genomic instability and myelodysplasia with monosomy 7 consequent to EVI1 activation after gene therapy for chronic granulomatous disease.
Stefan Stein, Marion G Ott, Stephan Schultze-Strasser, Anna Jauch, Barbara Burwinkel, Andrea Kinner, Manfred Schmidt, Alwin Krämer, Joachim Schwäble, Hanno Glimm,[...]. Nat Med 2010
568
11

Metachromatic leukodystrophy--an update.
V Gieselmann, I Krägeloh-Mann. Neuropediatrics 2010
101
11

Correction of metachromatic leukodystrophy in the mouse model by transplantation of genetically modified hematopoietic stem cells.
Alessandra Biffi, Michele De Palma, Angelo Quattrini, Ubaldo Del Carro, Stefano Amadio, Ilaria Visigalli, Maria Sessa, Stefania Fasano, Riccardo Brambilla, Sergio Marchesini,[...]. J Clin Invest 2004
220
11

Myeloid/Microglial driven autologous hematopoietic stem cell gene therapy corrects a neuronopathic lysosomal disease.
Ana Sergijenko, Alexander Langford-Smith, Ai Y Liao, Claire E Pickford, John McDermott, Gabriel Nowinski, Kia J Langford-Smith, Catherine L R Merry, Simon A Jones, J Edmond Wraith,[...]. Mol Ther 2013
77
12

Intracerebral gene therapy in children with mucopolysaccharidosis type IIIB syndrome: an uncontrolled phase 1/2 clinical trial.
Marc Tardieu, Michel Zérah, Marie-Lise Gougeon, Jérome Ausseil, Stéphanie de Bournonville, Béatrice Husson, Dimitrios Zafeiriou, Giancarlo Parenti, Philippe Bourget, Béatrice Poirier,[...]. Lancet Neurol 2017
98
10

CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cells.
Daniel P Dever, Rasmus O Bak, Andreas Reinisch, Joab Camarena, Gabriel Washington, Carmencita E Nicolas, Mara Pavel-Dinu, Nivi Saxena, Alec B Wilkens, Sruthi Mantri,[...]. Nature 2016
471
10

Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome.
Salima Hacein-Bey Abina, H Bobby Gaspar, Johanna Blondeau, Laure Caccavelli, Sabine Charrier, Karen Buckland, Capucine Picard, Emmanuelle Six, Nourredine Himoudi, Kimberly Gilmour,[...]. JAMA 2015
233
10

Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency.
Maria Pia Cicalese, Francesca Ferrua, Laura Castagnaro, Roberta Pajno, Federica Barzaghi, Stefania Giannelli, Francesca Dionisio, Immacolata Brigida, Marco Bonopane, Miriam Casiraghi,[...]. Blood 2016
120
10

Neurodevelopmental outcomes of umbilical cord blood transplantation in metachromatic leukodystrophy.
Holly R Martin, Michele D Poe, James M Provenzale, Joanne Kurtzberg, Adam Mendizabal, Maria L Escolar. Biol Blood Marrow Transplant 2013
70
14

Efficacy of hematopoietic cell transplantation in metachromatic leukodystrophy: the Dutch experience.
Diane F van Rappard, Jaap J Boelens, Martje E van Egmond, Jurgen Kuball, Peter M van Hasselt, Kim J Oostrom, Petra J W Pouwels, Marjo S van der Knaap, Carla E M Hollak, Nicole I Wolf. Blood 2016
34
29

Lysosomal storage diseases.
Frances M Platt, Alessandra d'Azzo, Beverly L Davidson, Elizabeth F Neufeld, Cynthia J Tifft. Nat Rev Dis Primers 2018
291
10

Gene therapy comes of age.
Cynthia E Dunbar, Katherine A High, J Keith Joung, Donald B Kohn, Keiya Ozawa, Michel Sadelain. Science 2018
538
9

Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1.
Salima Hacein-Bey-Abina, Alexandrine Garrigue, Gary P Wang, Jean Soulier, Annick Lim, Estelle Morillon, Emmanuelle Clappier, Laure Caccavelli, Eric Delabesse, Kheira Beldjord,[...]. J Clin Invest 2008
9

Hematopoietic Stem Cell Gene Therapy: Progress and Lessons Learned.
Richard A Morgan, David Gray, Anastasia Lomova, Donald B Kohn. Cell Stem Cell 2017
102
9

Search-and-replace genome editing without double-strand breaks or donor DNA.
Andrew V Anzalone, Peyton B Randolph, Jessie R Davis, Alexander A Sousa, Luke W Koblan, Jonathan M Levy, Peter J Chen, Christopher Wilson, Gregory A Newby, Aditya Raguram,[...]. Nature 2019
9

Gene therapy for immunodeficiency due to adenosine deaminase deficiency.
Alessandro Aiuti, Federica Cattaneo, Stefania Galimberti, Ulrike Benninghoff, Barbara Cassani, Luciano Callegaro, Samantha Scaramuzza, Grazia Andolfi, Massimiliano Mirolo, Immacolata Brigida,[...]. N Engl J Med 2009
676
9

Lentiviral Gene Therapy Combined with Low-Dose Busulfan in Infants with SCID-X1.
Ewelina Mamcarz, Sheng Zhou, Timothy Lockey, Hossam Abdelsamed, Shane J Cross, Guolian Kang, Zhijun Ma, Jose Condori, Jola Dowdy, Brandon Triplett,[...]. N Engl J Med 2019
110
9

Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1.
Marion G Ott, Manfred Schmidt, Kerstin Schwarzwaelder, Stefan Stein, Ulrich Siler, Ulrike Koehl, Hanno Glimm, Klaus Kühlcke, Andrea Schilz, Hana Kunkel,[...]. Nat Med 2006
866
9

Lentiviral hematopoietic stem cell gene therapy for X-linked severe combined immunodeficiency.
Suk See De Ravin, Xiaolin Wu, Susan Moir, Sandra Anaya-O'Brien, Nana Kwatemaa, Patricia Littel, Narda Theobald, Uimook Choi, Ling Su, Martha Marquesen,[...]. Sci Transl Med 2016
161
9

A third-generation lentivirus vector with a conditional packaging system.
T Dull, R Zufferey, M Kelly, R J Mandel, M Nguyen, D Trono, L Naldini. J Virol 1998
9


Gene Therapy in a Patient with Sickle Cell Disease.
Jean-Antoine Ribeil, Salima Hacein-Bey-Abina, Emmanuel Payen, Alessandra Magnani, Michaela Semeraro, Elisa Magrin, Laure Caccavelli, Benedicte Neven, Philippe Bourget, Wassim El Nemer,[...]. N Engl J Med 2017
395
9

Mutation Update of ARSA and PSAP Genes Causing Metachromatic Leukodystrophy.
Martina Cesani, Laura Lorioli, Serena Grossi, Giulia Amico, Francesca Fumagalli, Ivana Spiga, Mirella Filocamo, Alessandra Biffi. Hum Mutat 2016
55
16

Correction of brain oligodendrocytes by AAVrh.10 intracerebral gene therapy in metachromatic leukodystrophy mice.
Françoise Piguet, Dolan Sondhi, Monique Piraud, Françoise Fouquet, Neil R Hackett, Ornella Ahouansou, Marie-Thérèse Vanier, Ivan Bieche, Patrick Aubourg, Ronald G Crystal,[...]. Hum Gene Ther 2012
52
17

Association of Age at Onset and First Symptoms With Disease Progression in Patients With Metachromatic Leukodystrophy.
Christiane Kehrer, Saskia Elgün, Christa Raabe, Judith Böhringer, Stefanie Beck-Wödl, Andrea Bevot, Nadja Kaiser, Ludger Schöls, Ingeborg Krägeloh-Mann, Samuel Groeschel. Neurology 2021
17
52

The genotoxic potential of retroviral vectors is strongly modulated by vector design and integration site selection in a mouse model of HSC gene therapy.
Eugenio Montini, Daniela Cesana, Manfred Schmidt, Francesca Sanvito, Cynthia C Bartholomae, Marco Ranzani, Fabrizio Benedicenti, Lucia Sergi Sergi, Alessandro Ambrosi, Maurilio Ponzoni,[...]. J Clin Invest 2009
402
9


Co-cited is the co-citation frequency, indicating how many articles cite the article together with the query article. Similarity is the co-citation as percentage of the times cited of the query article or the article in the search results, whichever is the lowest. These numbers are calculated for the last 100 citations when articles are cited more than 100 times.