A citation-based method for searching scientific literature

Savita Rangarajan, Liron Walsh, Will Lester, David Perry, Bella Madan, Michael Laffan, Hua Yu, Christian Vettermann, Glenn F Pierce, Wing Y Wong, K John Pasi. N Engl J Med 2017
Times Cited: 364







List of co-cited articles
891 articles co-cited >1



Times Cited
  Times     Co-cited
Similarity


Long-term safety and efficacy of factor IX gene therapy in hemophilia B.
Amit C Nathwani, Ulreke M Reiss, Edward G D Tuddenham, Cecilia Rosales, Pratima Chowdary, Jenny McIntosh, Marco Della Peruta, Elsa Lheriteau, Nishal Patel, Deepak Raj,[...]. N Engl J Med 2014
762
51

Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant.
Lindsey A George, Spencer K Sullivan, Adam Giermasz, John E J Rasko, Benjamin J Samelson-Jones, Jonathan Ducore, Adam Cuker, Lisa M Sullivan, Suvankar Majumdar, Jerome Teitel,[...]. N Engl J Med 2017
372
51

Multiyear Follow-up of AAV5-hFVIII-SQ Gene Therapy for Hemophilia A.
K John Pasi, Savita Rangarajan, Nina Mitchell, Will Lester, Emily Symington, Bella Madan, Michael Laffan, Chris B Russell, Mingjin Li, Glenn F Pierce,[...]. N Engl J Med 2020
162
45

Adenovirus-associated virus vector-mediated gene transfer in hemophilia B.
Amit C Nathwani, Edward G D Tuddenham, Savita Rangarajan, Cecilia Rosales, Jenny McIntosh, David C Linch, Pratima Chowdary, Anne Riddell, Arnulfo Jaquilmac Pie, Chris Harrington,[...]. N Engl J Med 2011
39

Gene therapy with adeno-associated virus vector 5-human factor IX in adults with hemophilia B.
Wolfgang Miesbach, Karina Meijer, Michiel Coppens, Peter Kampmann, Robert Klamroth, Roger Schutgens, Marco Tangelder, Giancarlo Castaman, Joachim Schwäble, Halvard Bonig,[...]. Blood 2018
159
35

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response.
Catherine S Manno, Glenn F Pierce, Valder R Arruda, Bertil Glader, Margaret Ragni, John J Rasko, Margareth C Ozelo, Keith Hoots, Philip Blatt, Barbara Konkle,[...]. Nat Med 2006
32

Adeno-associated virus vector as a platform for gene therapy delivery.
Dan Wang, Phillip W L Tai, Guangping Gao. Nat Rev Drug Discov 2019
557
26

Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy.
Jerry R Mendell, Samiah Al-Zaidy, Richard Shell, W Dave Arnold, Louise R Rodino-Klapac, Thomas W Prior, Linda Lowes, Lindsay Alfano, Katherine Berry, Kathleen Church,[...]. N Engl J Med 2017
994
22

WFH Guidelines for the Management of Hemophilia, 3rd edition.
Alok Srivastava, Elena Santagostino, Alison Dougall, Steve Kitchen, Megan Sutherland, Steven W Pipe, Manuel Carcao, Johnny Mahlangu, Margaret V Ragni, Jerzy Windyga,[...]. Haemophilia 2020
326
19

Prevalence of serum IgG and neutralizing factors against adeno-associated virus (AAV) types 1, 2, 5, 6, 8, and 9 in the healthy population: implications for gene therapy using AAV vectors.
Sylvie Boutin, Virginie Monteilhet, Philippe Veron, Christian Leborgne, Olivier Benveniste, Marie Françoise Montus, Carole Masurier. Hum Gene Ther 2010
541
18

AAV Vector Immunogenicity in Humans: A Long Journey to Successful Gene Transfer.
Helena Costa Verdera, Klaudia Kuranda, Federico Mingozzi. Mol Ther 2020
141
17

Emicizumab Prophylaxis in Hemophilia A with Inhibitors.
Johannes Oldenburg, Johnny N Mahlangu, Benjamin Kim, Christophe Schmitt, Michael U Callaghan, Guy Young, Elena Santagostino, Rebecca Kruse-Jarres, Claude Negrier, Craig Kessler,[...]. N Engl J Med 2017
488
16

Prophylaxis versus episodic treatment to prevent joint disease in boys with severe hemophilia.
Marilyn J Manco-Johnson, Thomas C Abshire, Amy D Shapiro, Brenda Riske, Michele R Hacker, Ray Kilcoyne, J David Ingram, Michael L Manco-Johnson, Sharon Funk, Linda Jacobson,[...]. N Engl J Med 2007
15

Emicizumab Prophylaxis in Patients Who Have Hemophilia A without Inhibitors.
Johnny Mahlangu, Johannes Oldenburg, Ido Paz-Priel, Claude Negrier, Markus Niggli, M Elisa Mancuso, Christophe Schmitt, Victor Jiménez-Yuste, Christine Kempton, Christophe Dhalluin,[...]. N Engl J Med 2018
297
15

Worldwide epidemiology of neutralizing antibodies to adeno-associated viruses.
Roberto Calcedo, Luk H Vandenberghe, Guangping Gao, Jianping Lin, James M Wilson. J Infect Dis 2009
470
15

X-linked thrombophilia with a mutant factor IX (factor IX Padua).
Paolo Simioni, Daniela Tormene, Giulio Tognin, Sabrina Gavasso, Cristiana Bulato, Nicholas P Iacobelli, Jonathan D Finn, Luca Spiezia, Claudia Radu, Valder R Arruda. N Engl J Med 2009
200
14

Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant.
Jenny McIntosh, Peter J Lenting, Cecilia Rosales, Doyoung Lee, Samira Rabbanian, Deepak Raj, Nishil Patel, Edward G D Tuddenham, Olivier D Christophe, John H McVey,[...]. Blood 2013
181
14

CD8(+) T-cell responses to adeno-associated virus capsid in humans.
Federico Mingozzi, Marcela V Maus, Daniel J Hui, Denise E Sabatino, Samuel L Murphy, John E J Rasko, Margaret V Ragni, Catherine S Manno, Jurg Sommer, Haiyan Jiang,[...]. Nat Med 2007
489
13

Therapeutic hFIX Activity Achieved after Single AAV5-hFIX Treatment in Hemophilia B Patients and NHPs with Pre-existing Anti-AAV5 NABs.
Anna Majowicz, Bart Nijmeijer, Margit H Lampen, Lisa Spronck, Martin de Haan, Harald Petry, Sander J van Deventer, Christian Meyer, Marco Tangelder, Valerie Ferreira. Mol Ther Methods Clin Dev 2019
48
27

Emerging Issues in AAV-Mediated In Vivo Gene Therapy.
Pasqualina Colella, Giuseppe Ronzitti, Federico Mingozzi. Mol Ther Methods Clin Dev 2017
359
13

Long-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteins.
Amit C Nathwani, Cecilia Rosales, Jenny McIntosh, Ghasem Rastegarlari, Devhrut Nathwani, Deepak Raj, Sushmita Nawathe, Simon N Waddington, Roderick Bronson, Scott Jackson,[...]. Mol Ther 2011
210
13

Long-Term Follow-Up of the First in Human Intravascular Delivery of AAV for Gene Transfer: AAV2-hFIX16 for Severe Hemophilia B.
Lindsey A George, Margaret V Ragni, John E J Rasko, Leslie J Raffini, Benjamin J Samelson-Jones, Margareth Ozelo, Maria Hazbon, Alexa R Runowski, Jennifer A Wellman, Katie Wachtel,[...]. Mol Ther 2020
50
26

Update on clinical gene therapy for hemophilia.
George Q Perrin, Roland W Herzog, David M Markusic. Blood 2019
80
16


IgG-cleaving endopeptidase enables in vivo gene therapy in the presence of anti-AAV neutralizing antibodies.
Christian Leborgne, Elena Barbon, Jeffrey M Alexander, Hayley Hanby, Sandrine Delignat, Daniel M Cohen, Fanny Collaud, Saghana Muraleetharan, Dan Lupo, Joseph Silverberg,[...]. Nat Med 2020
88
13

Etranacogene dezaparvovec (AMT-061 phase 2b): normal/near normal FIX activity and bleed cessation in hemophilia B.
Annette Von Drygalski, Adam Giermasz, Giancarlo Castaman, Nigel S Key, Susan Lattimore, Frank W G Leebeek, Wolfgang Miesbach, Michael Recht, Alison Long, Robert Gut,[...]. Blood Adv 2019
31
35

AAV vector integration sites in mouse hepatocellular carcinoma.
Anthony Donsante, Daniel G Miller, Yi Li, Carole Vogler, Elizabeth M Brunt, David W Russell, Mark S Sands. Science 2007
414
11

Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial.
Stephen Russell, Jean Bennett, Jennifer A Wellman, Daniel C Chung, Zi-Fan Yu, Amy Tillman, Janet Wittes, Julie Pappas, Okan Elci, Sarah McCague,[...]. Lancet 2017
725
11

Advances and challenges for hemophilia gene therapy.
Paul Batty, David Lillicrap. Hum Mol Genet 2019
41
24

Recurrent AAV2-related insertional mutagenesis in human hepatocellular carcinomas.
Jean-Charles Nault, Shalini Datta, Sandrine Imbeaud, Andrea Franconi, Maxime Mallet, Gabrielle Couchy, Eric Letouzé, Camilla Pilati, Benjamin Verret, Jean-Frédéric Blanc,[...]. Nat Genet 2015
275
10

Selection and evaluation of clinically relevant AAV variants in a xenograft liver model.
Leszek Lisowski, Allison P Dane, Kirk Chu, Yue Zhang, Sharon C Cunningham, Elizabeth M Wilson, Sean Nygaard, Markus Grompe, Ian E Alexander, Mark A Kay. Nature 2014
265
10

BAX 335 hemophilia B gene therapy clinical trial results: potential impact of CpG sequences on gene expression.
Barbara A Konkle, Christopher E Walsh, Miguel A Escobar, Neil C Josephson, Guy Young, Annette von Drygalski, Scott W J McPhee, R Jude Samulski, Ivan Bilic, Maurus de la Rosa,[...]. Blood 2021
33
30

Guidelines for the management of hemophilia.
A Srivastava, A K Brewer, E P Mauser-Bunschoten, N S Key, S Kitchen, A Llinas, C A Ludlam, J N Mahlangu, K Mulder, M C Poon,[...]. Haemophilia 2013
9

Gene therapy for hemophilia.
Amit C Nathwani. Hematology Am Soc Hematol Educ Program 2019
44
20

Prevalence of Anti-Adeno-Associated Virus Immune Responses in International Cohorts of Healthy Donors.
Anita Kruzik, Damir Fetahagic, Bettina Hartlieb, Sebastian Dorn, Herwig Koppensteiner, Frank M Horling, Friedrich Scheiflinger, Birgit M Reipert, Maurus de la Rosa. Mol Ther Methods Clin Dev 2019
50
18

Recombinant AAV Integration Is Not Associated With Hepatic Genotoxicity in Nonhuman Primates and Patients.
Irene Gil-Farina, Raffaele Fronza, Christine Kaeppel, Esperanza Lopez-Franco, Valerie Ferreira, Delia D'Avola, Alberto Benito, Jesus Prieto, Harald Petry, Gloria Gonzalez-Aseguinolaza,[...]. Mol Ther 2016
79
11

AAV liver expression of FIX-Padua prevents and eradicates FIX inhibitor without increasing thrombogenicity in hemophilia B dogs and mice.
Julie M Crudele, Jonathan D Finn, Joshua I Siner, Nicholas B Martin, Glenn P Niemeyer, Shangzhen Zhou, Federico Mingozzi, Clinton D Lothrop, Valder R Arruda. Blood 2015
98
9

The Impact of Pre-existing Immunity on the Non-clinical Pharmacodynamics of AAV5-Based Gene Therapy.
Brian R Long, Krystal Sandza, Jennifer Holcomb, Lucy Crockett, Gregory M Hayes, Jeremy Arens, Carlos Fonck, Laurie S Tsuruda, Becky Schweighardt, Charles A O'Neill,[...]. Mol Ther Methods Clin Dev 2019
27
33

Vector design influences hepatic genotoxicity after adeno-associated virus gene therapy.
Randy J Chandler, Matthew C LaFave, Gaurav K Varshney, Niraj S Trivedi, Nuria Carrillo-Carrasco, Julien S Senac, Weiwei Wu, Victoria Hoffmann, Abdel G Elkahloun, Shawn M Burgess,[...]. J Clin Invest 2015
205
9

Pre-existing anti-adeno-associated virus antibodies as a challenge in AAV gene therapy.
Vedell Louis Jeune, Jakob A Joergensen, Roger J Hajjar, Thomas Weber. Hum Gene Ther Methods 2013
151
9

Neutralizing antibodies against adeno-associated virus examined prospectively in pediatric patients with hemophilia.
C Li, N Narkbunnam, R J Samulski, A Asokan, G Hu, L J Jacobson, M J Manco-Johnson, P E Monahan. Gene Ther 2012
132
9

The hemophilias--from royal genes to gene therapy.
P M Mannucci, E G Tuddenham. N Engl J Med 2001
684
9

Engineering adeno-associated virus vectors for gene therapy.
Chengwen Li, R Jude Samulski. Nat Rev Genet 2020
264
9

Comparative Study of Liver Gene Transfer With AAV Vectors Based on Natural and Engineered AAV Capsids.
Lili Wang, Peter Bell, Suryanarayan Somanathan, Qiang Wang, Zhenning He, Hongwei Yu, Deirdre McMenamin, Tamara Goode, Roberto Calcedo, James M Wilson. Mol Ther 2015
61
13

Exposure to wild-type AAV drives distinct capsid immunity profiles in humans.
Klaudia Kuranda, Priscilla Jean-Alphonse, Christian Leborgne, Romain Hardet, Fanny Collaud, Solenne Marmier, Helena Costa Verdera, Giuseppe Ronzitti, Philippe Veron, Federico Mingozzi. J Clin Invest 2018
50
16

Clinical severity of haemophilia A: does the classification of the 1950s still stand?
I E M Den Uijl, E P Mauser Bunschoten, G Roosendaal, R E G Schutgens, D H Biesma, D E Grobbee, K Fischer. Haemophilia 2011
158
8

Capsid-specific removal of circulating antibodies to adeno-associated virus vectors.
Berangere Bertin, Philippe Veron, Christian Leborgne, Jack-Yves Deschamps, Sophie Moullec, Yves Fromes, Fanny Collaud, Sylvie Boutin, Virginie Latournerie, Laetitia van Wittenberghe,[...]. Sci Rep 2020
35
22

Gene Therapy with BMN 270 Results in Therapeutic Levels of FVIII in Mice and Primates and Normalization of Bleeding in Hemophilic Mice.
Stuart Bunting, Lening Zhang, Lin Xie, Sherry Bullens, Rajeev Mahimkar, Sylvia Fong, Krystal Sandza, Danielle Harmon, Bridget Yates, Britta Handyside,[...]. Mol Ther 2018
31
25

Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman primate liver.
Amit C Nathwani, John T Gray, Catherine Y C Ng, Junfang Zhou, Yunyu Spence, Simon N Waddington, Edward G D Tuddenham, Geoffrey Kemball-Cook, Jenny McIntosh, Mariette Boon-Spijker,[...]. Blood 2006
306
8



Co-cited is the co-citation frequency, indicating how many articles cite the article together with the query article. Similarity is the co-citation as percentage of the times cited of the query article or the article in the search results, whichever is the lowest. These numbers are calculated for the last 100 citations when articles are cited more than 100 times.