Kunwoo Lee, Michael Conboy, Hyo Min Park, Fuguo Jiang, Hyun Jin Kim, Mark A Dewitt, Vanessa A Mackley, Kevin Chang, Anirudh Rao, Colin Skinner, Tamanna Shobha, Melod Mehdipour, Hui Liu, Wen-Chin Huang, Freeman Lan, Nicolas L Bray, Song Li, Jacob E Corn, Kazunori Kataoka, Jennifer A Doudna, Irina Conboy, Niren Murthy. Nat Biomed Eng 2017
Times Cited: 342
Times Cited: 342
Times Cited
Times Co-cited
Similarity
A programmable dual-RNA-guided DNA endonuclease in adaptive bacterial immunity.
Martin Jinek, Krzysztof Chylinski, Ines Fonfara, Michael Hauer, Jennifer A Doudna, Emmanuelle Charpentier. Science 2012
Martin Jinek, Krzysztof Chylinski, Ines Fonfara, Michael Hauer, Jennifer A Doudna, Emmanuelle Charpentier. Science 2012
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Multiplex genome engineering using CRISPR/Cas systems.
Le Cong, F Ann Ran, David Cox, Shuailiang Lin, Robert Barretto, Naomi Habib, Patrick D Hsu, Xuebing Wu, Wenyan Jiang, Luciano A Marraffini,[...]. Science 2013
Le Cong, F Ann Ran, David Cox, Shuailiang Lin, Robert Barretto, Naomi Habib, Patrick D Hsu, Xuebing Wu, Wenyan Jiang, Luciano A Marraffini,[...]. Science 2013
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RNA-guided human genome engineering via Cas9.
Prashant Mali, Luhan Yang, Kevin M Esvelt, John Aach, Marc Guell, James E DiCarlo, Julie E Norville, George M Church. Science 2013
Prashant Mali, Luhan Yang, Kevin M Esvelt, John Aach, Marc Guell, James E DiCarlo, Julie E Norville, George M Church. Science 2013
27
Cationic lipid-mediated delivery of proteins enables efficient protein-based genome editing in vitro and in vivo.
John A Zuris, David B Thompson, Yilai Shu, John P Guilinger, Jeffrey L Bessen, Johnny H Hu, Morgan L Maeder, J Keith Joung, Zheng-Yi Chen, David R Liu. Nat Biotechnol 2015
John A Zuris, David B Thompson, Yilai Shu, John P Guilinger, Jeffrey L Bessen, Johnny H Hu, Morgan L Maeder, J Keith Joung, Zheng-Yi Chen, David R Liu. Nat Biotechnol 2015
27
Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo.
Hao Yin, Chun-Qing Song, Joseph R Dorkin, Lihua J Zhu, Yingxiang Li, Qiongqiong Wu, Angela Park, Junghoon Yang, Sneha Suresh, Aizhan Bizhanova,[...]. Nat Biotechnol 2016
Hao Yin, Chun-Qing Song, Joseph R Dorkin, Lihua J Zhu, Yingxiang Li, Qiongqiong Wu, Angela Park, Junghoon Yang, Sneha Suresh, Aizhan Bizhanova,[...]. Nat Biotechnol 2016
26
Search-and-replace genome editing without double-strand breaks or donor DNA.
Andrew V Anzalone, Peyton B Randolph, Jessie R Davis, Alexander A Sousa, Luke W Koblan, Jonathan M Levy, Peter J Chen, Christopher Wilson, Gregory A Newby, Aditya Raguram,[...]. Nature 2019
Andrew V Anzalone, Peyton B Randolph, Jessie R Davis, Alexander A Sousa, Luke W Koblan, Jonathan M Levy, Peter J Chen, Christopher Wilson, Gregory A Newby, Aditya Raguram,[...]. Nature 2019
26
Programmable editing of a target base in genomic DNA without double-stranded DNA cleavage.
Alexis C Komor, Yongjoo B Kim, Michael S Packer, John A Zuris, David R Liu. Nature 2016
Alexis C Komor, Yongjoo B Kim, Michael S Packer, John A Zuris, David R Liu. Nature 2016
25
Direct Cytosolic Delivery of CRISPR/Cas9-Ribonucleoprotein for Efficient Gene Editing.
Rubul Mout, Moumita Ray, Gulen Yesilbag Tonga, Yi-Wei Lee, Tristan Tay, Kanae Sasaki, Vincent M Rotello. ACS Nano 2017
Rubul Mout, Moumita Ray, Gulen Yesilbag Tonga, Yi-Wei Lee, Tristan Tay, Kanae Sasaki, Vincent M Rotello. ACS Nano 2017
23
A Single Administration of CRISPR/Cas9 Lipid Nanoparticles Achieves Robust and Persistent In Vivo Genome Editing.
Jonathan D Finn, Amy Rhoden Smith, Mihir C Patel, Lucinda Shaw, Madeleine R Youniss, Jane van Heteren, Tanner Dirstine, Corey Ciullo, Reynald Lescarbeau, Jessica Seitzer,[...]. Cell Rep 2018
Jonathan D Finn, Amy Rhoden Smith, Mihir C Patel, Lucinda Shaw, Madeleine R Youniss, Jane van Heteren, Tanner Dirstine, Corey Ciullo, Reynald Lescarbeau, Jessica Seitzer,[...]. Cell Rep 2018
23
Nanoparticle delivery of CRISPR into the brain rescues a mouse model of fragile X syndrome from exaggerated repetitive behaviours.
Bumwhee Lee, Kunwoo Lee, Shree Panda, Rodrigo Gonzales-Rojas, Anthony Chong, Vladislav Bugay, Hyo Min Park, Robert Brenner, Niren Murthy, Hye Young Lee. Nat Biomed Eng 2018
Bumwhee Lee, Kunwoo Lee, Shree Panda, Rodrigo Gonzales-Rojas, Anthony Chong, Vladislav Bugay, Hyo Min Park, Robert Brenner, Niren Murthy, Hye Young Lee. Nat Biomed Eng 2018
23
Non-Viral CRISPR/Cas Gene Editing In Vitro and In Vivo Enabled by Synthetic Nanoparticle Co-Delivery of Cas9 mRNA and sgRNA.
Jason B Miller, Shuyuan Zhang, Petra Kos, Hu Xiong, Kejin Zhou, Sofya S Perelman, Hao Zhu, Daniel J Siegwart. Angew Chem Int Ed Engl 2017
Jason B Miller, Shuyuan Zhang, Petra Kos, Hu Xiong, Kejin Zhou, Sofya S Perelman, Hao Zhu, Daniel J Siegwart. Angew Chem Int Ed Engl 2017
23
Identification of preexisting adaptive immunity to Cas9 proteins in humans.
Carsten T Charlesworth, Priyanka S Deshpande, Daniel P Dever, Joab Camarena, Viktor T Lemgart, M Kyle Cromer, Christopher A Vakulskas, Michael A Collingwood, Liyang Zhang, Nicole M Bode,[...]. Nat Med 2019
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22
Development and applications of CRISPR-Cas9 for genome engineering.
Patrick D Hsu, Eric S Lander, Feng Zhang. Cell 2014
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21
Efficient delivery of genome-editing proteins using bioreducible lipid nanoparticles.
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21
Self-assembled DNA nanoclews for the efficient delivery of CRISPR-Cas9 for genome editing.
Wujin Sun, Wenyan Ji, Jordan M Hall, Quanyin Hu, Chao Wang, Chase L Beisel, Zhen Gu. Angew Chem Int Ed Engl 2015
Wujin Sun, Wenyan Ji, Jordan M Hall, Quanyin Hu, Chao Wang, Chase L Beisel, Zhen Gu. Angew Chem Int Ed Engl 2015
21
A non-viral CRISPR/Cas9 delivery system for therapeutically targeting HBV DNA and pcsk9 in vivo.
Chao Jiang, Miao Mei, Bin Li, Xiurui Zhu, Wenhong Zu, Yujie Tian, Qiannan Wang, Yong Guo, Yizhou Dong, Xu Tan. Cell Res 2017
Chao Jiang, Miao Mei, Bin Li, Xiurui Zhu, Wenhong Zu, Yujie Tian, Qiannan Wang, Yong Guo, Yizhou Dong, Xu Tan. Cell Res 2017
20
Programmable base editing of A•T to G•C in genomic DNA without DNA cleavage.
Nicole M Gaudelli, Alexis C Komor, Holly A Rees, Michael S Packer, Ahmed H Badran, David I Bryson, David R Liu. Nature 2017
Nicole M Gaudelli, Alexis C Komor, Holly A Rees, Michael S Packer, Ahmed H Badran, David I Bryson, David R Liu. Nature 2017
20
Structure-guided chemical modification of guide RNA enables potent non-viral in vivo genome editing.
Hao Yin, Chun-Qing Song, Sneha Suresh, Qiongqiong Wu, Stephen Walsh, Luke Hyunsik Rhym, Esther Mintzer, Mehmet Fatih Bolukbasi, Lihua Julie Zhu, Kevin Kauffman,[...]. Nat Biotechnol 2017
Hao Yin, Chun-Qing Song, Sneha Suresh, Qiongqiong Wu, Stephen Walsh, Luke Hyunsik Rhym, Esther Mintzer, Mehmet Fatih Bolukbasi, Lihua Julie Zhu, Kevin Kauffman,[...]. Nat Biotechnol 2017
18
Delivering CRISPR: a review of the challenges and approaches.
Christopher A Lino, Jason C Harper, James P Carney, Jerilyn A Timlin. Drug Deliv 2018
Christopher A Lino, Jason C Harper, James P Carney, Jerilyn A Timlin. Drug Deliv 2018
18
Highly efficient RNA-guided genome editing in human cells via delivery of purified Cas9 ribonucleoproteins.
Sojung Kim, Daesik Kim, Seung Woo Cho, Jungeun Kim, Jin-Soo Kim. Genome Res 2014
Sojung Kim, Daesik Kim, Seung Woo Cho, Jungeun Kim, Jin-Soo Kim. Genome Res 2014
18
Cas9-crRNA ribonucleoprotein complex mediates specific DNA cleavage for adaptive immunity in bacteria.
Giedrius Gasiunas, Rodolphe Barrangou, Philippe Horvath, Virginijus Siksnys. Proc Natl Acad Sci U S A 2012
Giedrius Gasiunas, Rodolphe Barrangou, Philippe Horvath, Virginijus Siksnys. Proc Natl Acad Sci U S A 2012
18
In vivo genome editing using Staphylococcus aureus Cas9.
F Ann Ran, Le Cong, Winston X Yan, David A Scott, Jonathan S Gootenberg, Andrea J Kriz, Bernd Zetsche, Ophir Shalem, Xuebing Wu, Kira S Makarova,[...]. Nature 2015
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18
Enhanced homology-directed human genome engineering by controlled timing of CRISPR/Cas9 delivery.
Steven Lin, Brett T Staahl, Ravi K Alla, Jennifer A Doudna. Elife 2014
Steven Lin, Brett T Staahl, Ravi K Alla, Jennifer A Doudna. Elife 2014
18
Systemic nanoparticle delivery of CRISPR-Cas9 ribonucleoproteins for effective tissue specific genome editing.
Tuo Wei, Qiang Cheng, Yi-Li Min, Eric N Olson, Daniel J Siegwart. Nat Commun 2020
Tuo Wei, Qiang Cheng, Yi-Li Min, Eric N Olson, Daniel J Siegwart. Nat Commun 2020
18
CRISPR provides acquired resistance against viruses in prokaryotes.
Rodolphe Barrangou, Christophe Fremaux, Hélène Deveau, Melissa Richards, Patrick Boyaval, Sylvain Moineau, Dennis A Romero, Philippe Horvath. Science 2007
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17
Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy.
Christopher E Nelson, Yaoying Wu, Matthew P Gemberling, Matthew L Oliver, Matthew A Waller, Joel D Bohning, Jacqueline N Robinson-Hamm, Karen Bulaklak, Ruth M Castellanos Rivera, Joel H Collier,[...]. Nat Med 2019
Christopher E Nelson, Yaoying Wu, Matthew P Gemberling, Matthew L Oliver, Matthew A Waller, Joel D Bohning, Jacqueline N Robinson-Hamm, Karen Bulaklak, Ruth M Castellanos Rivera, Joel H Collier,[...]. Nat Med 2019
17
Targeted homology-directed repair in blood stem and progenitor cells with CRISPR nanoformulations.
Reza Shahbazi, Gabriella Sghia-Hughes, Jack L Reid, Sara Kubek, Kevin G Haworth, Olivier Humbert, Hans-Peter Kiem, Jennifer E Adair. Nat Mater 2019
Reza Shahbazi, Gabriella Sghia-Hughes, Jack L Reid, Sara Kubek, Kevin G Haworth, Olivier Humbert, Hans-Peter Kiem, Jennifer E Adair. Nat Mater 2019
30
Therapeutic genome editing: prospects and challenges.
David Benjamin Turitz Cox, Randall Jeffrey Platt, Feng Zhang. Nat Med 2015
David Benjamin Turitz Cox, Randall Jeffrey Platt, Feng Zhang. Nat Med 2015
16
Genome editing. The new frontier of genome engineering with CRISPR-Cas9.
Jennifer A Doudna, Emmanuelle Charpentier. Science 2014
Jennifer A Doudna, Emmanuelle Charpentier. Science 2014
16
Thermo-triggered Release of CRISPR-Cas9 System by Lipid-Encapsulated Gold Nanoparticles for Tumor Therapy.
Peng Wang, Lingmin Zhang, Wenfu Zheng, Liman Cong, Zhaorong Guo, Yangzhouyun Xie, Le Wang, Rongbing Tang, Qiang Feng, Yoh Hamada,[...]. Angew Chem Int Ed Engl 2018
Peng Wang, Lingmin Zhang, Wenfu Zheng, Liman Cong, Zhaorong Guo, Yangzhouyun Xie, Le Wang, Rongbing Tang, Qiang Feng, Yoh Hamada,[...]. Angew Chem Int Ed Engl 2018
15
In vivo gene editing in dystrophic mouse muscle and muscle stem cells.
Mohammadsharif Tabebordbar, Kexian Zhu, Jason K W Cheng, Wei Leong Chew, Jeffrey J Widrick, Winston X Yan, Claire Maesner, Elizabeth Y Wu, Ru Xiao, F Ann Ran,[...]. Science 2016
Mohammadsharif Tabebordbar, Kexian Zhu, Jason K W Cheng, Wei Leong Chew, Jeffrey J Widrick, Winston X Yan, Claire Maesner, Elizabeth Y Wu, Ru Xiao, F Ann Ran,[...]. Science 2016
15
Cpf1 is a single RNA-guided endonuclease of a class 2 CRISPR-Cas system.
Bernd Zetsche, Jonathan S Gootenberg, Omar O Abudayyeh, Ian M Slaymaker, Kira S Makarova, Patrick Essletzbichler, Sara E Volz, Julia Joung, John van der Oost, Aviv Regev,[...]. Cell 2015
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15
In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy.
Christopher E Nelson, Chady H Hakim, David G Ousterout, Pratiksha I Thakore, Eirik A Moreb, Ruth M Castellanos Rivera, Sarina Madhavan, Xiufang Pan, F Ann Ran, Winston X Yan,[...]. Science 2016
Christopher E Nelson, Chady H Hakim, David G Ousterout, Pratiksha I Thakore, Eirik A Moreb, Ruth M Castellanos Rivera, Sarina Madhavan, Xiufang Pan, F Ann Ran, Winston X Yan,[...]. Science 2016
15
Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy.
Chengzu Long, Leonela Amoasii, Alex A Mireault, John R McAnally, Hui Li, Efrain Sanchez-Ortiz, Samadrita Bhattacharyya, John M Shelton, Rhonda Bassel-Duby, Eric N Olson. Science 2016
Chengzu Long, Leonela Amoasii, Alex A Mireault, John R McAnally, Hui Li, Efrain Sanchez-Ortiz, Samadrita Bhattacharyya, John M Shelton, Rhonda Bassel-Duby, Eric N Olson. Science 2016
15
Delivery strategies of the CRISPR-Cas9 gene-editing system for therapeutic applications.
Chang Liu, Li Zhang, Hao Liu, Kun Cheng. J Control Release 2017
Chang Liu, Li Zhang, Hao Liu, Kun Cheng. J Control Release 2017
15
Fast and Efficient CRISPR/Cas9 Genome Editing In Vivo Enabled by Bioreducible Lipid and Messenger RNA Nanoparticles.
Ji Liu, Jin Chang, Ying Jiang, Xiandi Meng, Tianmeng Sun, Lanqun Mao, Qiaobing Xu, Ming Wang. Adv Mater 2019
Ji Liu, Jin Chang, Ying Jiang, Xiandi Meng, Tianmeng Sun, Lanqun Mao, Qiaobing Xu, Ming Wang. Adv Mater 2019
14
Gene disruption by cell-penetrating peptide-mediated delivery of Cas9 protein and guide RNA.
Suresh Ramakrishna, Abu-Bonsrah Kwaku Dad, Jagadish Beloor, Ramu Gopalappa, Sang-Kyung Lee, Hyongbum Kim. Genome Res 2014
Suresh Ramakrishna, Abu-Bonsrah Kwaku Dad, Jagadish Beloor, Ramu Gopalappa, Sang-Kyung Lee, Hyongbum Kim. Genome Res 2014
14
High-fidelity CRISPR-Cas9 nucleases with no detectable genome-wide off-target effects.
Benjamin P Kleinstiver, Vikram Pattanayak, Michelle S Prew, Shengdar Q Tsai, Nhu T Nguyen, Zongli Zheng, J Keith Joung. Nature 2016
Benjamin P Kleinstiver, Vikram Pattanayak, Michelle S Prew, Shengdar Q Tsai, Nhu T Nguyen, Zongli Zheng, J Keith Joung. Nature 2016
14
Non-viral vectors for gene-based therapy.
Hao Yin, Rosemary L Kanasty, Ahmed A Eltoukhy, Arturo J Vegas, J Robert Dorkin, Daniel G Anderson. Nat Rev Genet 2014
Hao Yin, Rosemary L Kanasty, Ahmed A Eltoukhy, Arturo J Vegas, J Robert Dorkin, Daniel G Anderson. Nat Rev Genet 2014
14
Selective organ targeting (SORT) nanoparticles for tissue-specific mRNA delivery and CRISPR-Cas gene editing.
Qiang Cheng, Tuo Wei, Lukas Farbiak, Lindsay T Johnson, Sean A Dilliard, Daniel J Siegwart. Nat Nanotechnol 2020
Qiang Cheng, Tuo Wei, Lukas Farbiak, Lindsay T Johnson, Sean A Dilliard, Daniel J Siegwart. Nat Nanotechnol 2020
14
ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering.
Thomas Gaj, Charles A Gersbach, Carlos F Barbas. Trends Biotechnol 2013
Thomas Gaj, Charles A Gersbach, Carlos F Barbas. Trends Biotechnol 2013
14
Nucleotide sequence of the iap gene, responsible for alkaline phosphatase isozyme conversion in Escherichia coli, and identification of the gene product.
Y Ishino, H Shinagawa, K Makino, M Amemura, A Nakata. J Bacteriol 1987
Y Ishino, H Shinagawa, K Makino, M Amemura, A Nakata. J Bacteriol 1987
13
Endosomal Escape and Delivery of CRISPR/Cas9 Genome Editing Machinery Enabled by Nanoscale Zeolitic Imidazolate Framework.
Shahad K Alsaiari, Sachin Patil, Mram Alyami, Kholod O Alamoudi, Fajr A Aleisa, Jasmeen S Merzaban, Mo Li, Niveen M Khashab. J Am Chem Soc 2018
Shahad K Alsaiari, Sachin Patil, Mram Alyami, Kholod O Alamoudi, Fajr A Aleisa, Jasmeen S Merzaban, Mo Li, Niveen M Khashab. J Am Chem Soc 2018
13
Macrophage-Specific in Vivo Gene Editing Using Cationic Lipid-Assisted Polymeric Nanoparticles.
Ying-Li Luo, Cong-Fei Xu, Hong-Jun Li, Zhi-Ting Cao, Jing Liu, Ji-Long Wang, Xiao-Jiao Du, Xian-Zhu Yang, Zhen Gu, Jun Wang. ACS Nano 2018
Ying-Li Luo, Cong-Fei Xu, Hong-Jun Li, Zhi-Ting Cao, Jing Liu, Ji-Long Wang, Xiao-Jiao Du, Xian-Zhu Yang, Zhen Gu, Jun Wang. ACS Nano 2018
14
Non-viral delivery systems for CRISPR/Cas9-based genome editing: Challenges and opportunities.
Ling Li, Shuo Hu, Xiaoyuan Chen. Biomaterials 2018
Ling Li, Shuo Hu, Xiaoyuan Chen. Biomaterials 2018
13
A biodegradable nanocapsule delivers a Cas9 ribonucleoprotein complex for in vivo genome editing.
Guojun Chen, Amr A Abdeen, Yuyuan Wang, Pawan K Shahi, Samantha Robertson, Ruosen Xie, Masatoshi Suzuki, Bikash R Pattnaik, Krishanu Saha, Shaoqin Gong. Nat Nanotechnol 2019
Guojun Chen, Amr A Abdeen, Yuyuan Wang, Pawan K Shahi, Samantha Robertson, Ruosen Xie, Masatoshi Suzuki, Bikash R Pattnaik, Krishanu Saha, Shaoqin Gong. Nat Nanotechnol 2019
13
CRISPR-mediated modular RNA-guided regulation of transcription in eukaryotes.
Luke A Gilbert, Matthew H Larson, Leonardo Morsut, Zairan Liu, Gloria A Brar, Sandra E Torres, Noam Stern-Ginossar, Onn Brandman, Evan H Whitehead, Jennifer A Doudna,[...]. Cell 2013
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13
Rapid and highly efficient mammalian cell engineering via Cas9 protein transfection.
Xiquan Liang, Jason Potter, Shantanu Kumar, Yanfei Zou, Rene Quintanilla, Mahalakshmi Sridharan, Jason Carte, Wen Chen, Natasha Roark, Sridhar Ranganathan,[...]. J Biotechnol 2015
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13
Repair of double-strand breaks induced by CRISPR-Cas9 leads to large deletions and complex rearrangements.
Michael Kosicki, Kärt Tomberg, Allan Bradley. Nat Biotechnol 2018
Michael Kosicki, Kärt Tomberg, Allan Bradley. Nat Biotechnol 2018
13
CRISPR-Cas9 corrects Duchenne muscular dystrophy exon 44 deletion mutations in mice and human cells.
Yi-Li Min, Hui Li, Cristina Rodriguez-Caycedo, Alex A Mireault, Jian Huang, John M Shelton, John R McAnally, Leonela Amoasii, Pradeep P A Mammen, Rhonda Bassel-Duby,[...]. Sci Adv 2019
Yi-Li Min, Hui Li, Cristina Rodriguez-Caycedo, Alex A Mireault, Jian Huang, John M Shelton, John R McAnally, Leonela Amoasii, Pradeep P A Mammen, Rhonda Bassel-Duby,[...]. Sci Adv 2019
13
Co-cited is the co-citation frequency, indicating how many articles cite the article together with the query article. Similarity is the co-citation as percentage of the times cited of the query article or the article in the search results, whichever is the lowest. These numbers are calculated for the last 100 citations when articles are cited more than 100 times.