Ioannis S Dimopoulos, Stephanie C Hoang, Alina Radziwon, Natalia M Binczyk, Miguel C Seabra, Robert E MacLaren, Rizwan Somani, Matthew T S Tennant, Ian M MacDonald. Am J Ophthalmol 2018
Times Cited: 95
Times Cited: 95
Times Cited
Times Co-cited
Similarity
Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial.
Robert E MacLaren, Markus Groppe, Alun R Barnard, Charles L Cottriall, Tanya Tolmachova, Len Seymour, K Reed Clark, Matthew J During, Frans P M Cremers, Graeme C M Black,[...]. Lancet 2014
Robert E MacLaren, Markus Groppe, Alun R Barnard, Charles L Cottriall, Tanya Tolmachova, Len Seymour, K Reed Clark, Matthew J During, Frans P M Cremers, Graeme C M Black,[...]. Lancet 2014
65
Choroideremia Gene Therapy Phase 2 Clinical Trial: 24-Month Results.
Byron L Lam, Janet L Davis, Ninel Z Gregori, Robert E MacLaren, Aniz Girach, Jennifer D Verriotto, Belen Rodriguez, Potyra R Rosa, Xiaojun Zhang, William J Feuer. Am J Ophthalmol 2019
Byron L Lam, Janet L Davis, Ninel Z Gregori, Robert E MacLaren, Aniz Girach, Jennifer D Verriotto, Belen Rodriguez, Potyra R Rosa, Xiaojun Zhang, William J Feuer. Am J Ophthalmol 2019
71
Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial.
Stephen Russell, Jean Bennett, Jennifer A Wellman, Daniel C Chung, Zi-Fan Yu, Amy Tillman, Janet Wittes, Julie Pappas, Okan Elci, Sarah McCague,[...]. Lancet 2017
Stephen Russell, Jean Bennett, Jennifer A Wellman, Daniel C Chung, Zi-Fan Yu, Amy Tillman, Janet Wittes, Julie Pappas, Okan Elci, Sarah McCague,[...]. Lancet 2017
51
Beneficial effects on vision in patients undergoing retinal gene therapy for choroideremia.
Kanmin Xue, Jasleen K Jolly, Alun R Barnard, Anna Rudenko, Anna P Salvetti, Maria I Patrício, Thomas L Edwards, Markus Groppe, Harry O Orlans, Tanya Tolmachova,[...]. Nat Med 2018
Kanmin Xue, Jasleen K Jolly, Alun R Barnard, Anna Rudenko, Anna P Salvetti, Maria I Patrício, Thomas L Edwards, Markus Groppe, Harry O Orlans, Tanya Tolmachova,[...]. Nat Med 2018
44
Visual Acuity after Retinal Gene Therapy for Choroideremia.
Thomas L Edwards, Jasleen K Jolly, Markus Groppe, Alun R Barnard, Charles L Cottriall, Tanya Tolmachova, Graeme C Black, Andrew R Webster, Andrew J Lotery, Graham E Holder,[...]. N Engl J Med 2016
Thomas L Edwards, Jasleen K Jolly, Markus Groppe, Alun R Barnard, Charles L Cottriall, Tanya Tolmachova, Graeme C Black, Andrew R Webster, Andrew J Lotery, Graham E Holder,[...]. N Engl J Med 2016
38
Long-term effect of gene therapy on Leber's congenital amaurosis.
James W B Bainbridge, Manjit S Mehat, Venki Sundaram, Scott J Robbie, Susie E Barker, Caterina Ripamonti, Anastasios Georgiadis, Freya M Mowat, Stuart G Beattie, Peter J Gardner,[...]. N Engl J Med 2015
James W B Bainbridge, Manjit S Mehat, Venki Sundaram, Scott J Robbie, Susie E Barker, Caterina Ripamonti, Anastasios Georgiadis, Freya M Mowat, Stuart G Beattie, Peter J Gardner,[...]. N Engl J Med 2015
38
Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery.
Catherine Cukras, Henry E Wiley, Brett G Jeffrey, H Nida Sen, Amy Turriff, Yong Zeng, Camasamudram Vijayasarathy, Dario Marangoni, Lucia Ziccardi, Sten Kjellstrom,[...]. Mol Ther 2018
Catherine Cukras, Henry E Wiley, Brett G Jeffrey, H Nida Sen, Amy Turriff, Yong Zeng, Camasamudram Vijayasarathy, Dario Marangoni, Lucia Ziccardi, Sten Kjellstrom,[...]. Mol Ther 2018
35
Safety and efficacy of gene transfer for Leber's congenital amaurosis.
Albert M Maguire, Francesca Simonelli, Eric A Pierce, Edward N Pugh, Federico Mingozzi, Jeannette Bennicelli, Sandro Banfi, Kathleen A Marshall, Francesco Testa, Enrico M Surace,[...]. N Engl J Med 2008
Albert M Maguire, Francesca Simonelli, Eric A Pierce, Edward N Pugh, Federico Mingozzi, Jeannette Bennicelli, Sandro Banfi, Kathleen A Marshall, Francesco Testa, Enrico M Surace,[...]. N Engl J Med 2008
33
Efficacy and Safety of Retinal Gene Therapy Using Adeno-Associated Virus Vector for Patients With Choroideremia: A Randomized Clinical Trial.
M Dominik Fischer, G Alex Ochakovski, Benjamin Beier, Immanuel P Seitz, Yousof Vaheb, Constanze Kortuem, Felix F L Reichel, Laura Kuehlewein, Nadine A Kahle, Tobias Peters,[...]. JAMA Ophthalmol 2019
M Dominik Fischer, G Alex Ochakovski, Benjamin Beier, Immanuel P Seitz, Yousof Vaheb, Constanze Kortuem, Felix F L Reichel, Laura Kuehlewein, Nadine A Kahle, Tobias Peters,[...]. JAMA Ophthalmol 2019
63
CHANGES IN RETINAL SENSITIVITY AFTER GENE THERAPY IN CHOROIDEREMIA.
M Dominik Fischer, G Alex Ochakovski, Benjamin Beier, Immanuel P Seitz, Yousof Vaheb, Constanze Kortuem, Felix F L Reichel, Laura Kuehlewein, Nadine A Kahle, Tobias Peters,[...]. Retina 2020
M Dominik Fischer, G Alex Ochakovski, Benjamin Beier, Immanuel P Seitz, Yousof Vaheb, Constanze Kortuem, Felix F L Reichel, Laura Kuehlewein, Nadine A Kahle, Tobias Peters,[...]. Retina 2020
76
Effect of gene therapy on visual function in Leber's congenital amaurosis.
James W B Bainbridge, Alexander J Smith, Susie S Barker, Scott Robbie, Robert Henderson, Kamaljit Balaggan, Ananth Viswanathan, Graham E Holder, Andrew Stockman, Nick Tyler,[...]. N Engl J Med 2008
James W B Bainbridge, Alexander J Smith, Susie S Barker, Scott Robbie, Robert Henderson, Kamaljit Balaggan, Ananth Viswanathan, Graham E Holder, Andrew Stockman, Nick Tyler,[...]. N Engl J Med 2008
24
Technique of retinal gene therapy: delivery of viral vector into the subretinal space.
K Xue, M Groppe, A P Salvetti, R E MacLaren. Eye (Lond) 2017
K Xue, M Groppe, A P Salvetti, R E MacLaren. Eye (Lond) 2017
26
Safety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutations: a follow-on phase 1 trial.
Jean Bennett, Jennifer Wellman, Kathleen A Marshall, Sarah McCague, Manzar Ashtari, Julie DiStefano-Pappas, Okan U Elci, Daniel C Chung, Junwei Sun, J Fraser Wright,[...]. Lancet 2016
Jean Bennett, Jennifer Wellman, Kathleen A Marshall, Sarah McCague, Manzar Ashtari, Julie DiStefano-Pappas, Okan U Elci, Daniel C Chung, Junwei Sun, J Fraser Wright,[...]. Lancet 2016
23
Treatment of retinitis pigmentosa due to MERTK mutations by ocular subretinal injection of adeno-associated virus gene vector: results of a phase I trial.
Nicola G Ghazi, Emad B Abboud, Sawsan R Nowilaty, Hisham Alkuraya, Abdulrahman Alhommadi, Huimin Cai, Rui Hou, Wen-Tao Deng, Sanford L Boye, Abdulrahman Almaghamsi,[...]. Hum Genet 2016
Nicola G Ghazi, Emad B Abboud, Sawsan R Nowilaty, Hisham Alkuraya, Abdulrahman Alhommadi, Huimin Cai, Rui Hou, Wen-Tao Deng, Sanford L Boye, Abdulrahman Almaghamsi,[...]. Hum Genet 2016
23
Retinal degeneration in choroideremia: deficiency of rab geranylgeranyl transferase.
M C Seabra, M S Brown, J L Goldstein. Science 1993
M C Seabra, M S Brown, J L Goldstein. Science 1993
22
Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial.
Albert M Maguire, Katherine A High, Alberto Auricchio, J Fraser Wright, Eric A Pierce, Francesco Testa, Federico Mingozzi, Jeannette L Bennicelli, Gui-shuang Ying, Settimio Rossi,[...]. Lancet 2009
Albert M Maguire, Katherine A High, Alberto Auricchio, J Fraser Wright, Eric A Pierce, Francesco Testa, Federico Mingozzi, Jeannette L Bennicelli, Gui-shuang Ying, Settimio Rossi,[...]. Lancet 2009
21
Natural History of the Central Structural Abnormalities in Choroideremia: A Prospective Cross-Sectional Study.
Tomas S Aleman, Grace Han, Leona W Serrano, Nicole M Fuerst, Emily S Charlson, Denise J Pearson, Daniel C Chung, Anastasia Traband, Wei Pan, Gui-Shuang Ying,[...]. Ophthalmology 2017
Tomas S Aleman, Grace Han, Leona W Serrano, Nicole M Fuerst, Emily S Charlson, Denise J Pearson, Daniel C Chung, Anastasia Traband, Wei Pan, Gui-Shuang Ying,[...]. Ophthalmology 2017
27
Cloning of a gene that is rearranged in patients with choroideraemia.
F P Cremers, D J van de Pol, L P van Kerkhoff, B Wieringa, H H Ropers. Nature 1990
F P Cremers, D J van de Pol, L P van Kerkhoff, B Wieringa, H H Ropers. Nature 1990
21
Characterizing the Natural History of Visual Function in Choroideremia Using Microperimetry and Multimodal Retinal Imaging.
Jasleen K Jolly, Kanmin Xue, Thomas L Edwards, Markus Groppe, Robert E MacLaren. Invest Ophthalmol Vis Sci 2017
Jasleen K Jolly, Kanmin Xue, Thomas L Edwards, Markus Groppe, Robert E MacLaren. Invest Ophthalmol Vis Sci 2017
33
Efficacy, Safety, and Durability of Voretigene Neparvovec-rzyl in RPE65 Mutation-Associated Inherited Retinal Dystrophy: Results of Phase 1 and 3 Trials.
Albert M Maguire, Stephen Russell, Jennifer A Wellman, Daniel C Chung, Zi-Fan Yu, Amy Tillman, Janet Wittes, Julie Pappas, Okan Elci, Kathleen A Marshall,[...]. Ophthalmology 2019
Albert M Maguire, Stephen Russell, Jennifer A Wellman, Daniel C Chung, Zi-Fan Yu, Amy Tillman, Janet Wittes, Julie Pappas, Okan Elci, Kathleen A Marshall,[...]. Ophthalmology 2019
21
Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR.
Jasmina Cehajic-Kapetanovic, Kanmin Xue, Cristina Martinez-Fernandez de la Camara, Anika Nanda, Alexandra Davies, Laura J Wood, Anna Paola Salvetti, M Dominik Fischer, James W Aylward, Alun R Barnard,[...]. Nat Med 2020
Jasmina Cehajic-Kapetanovic, Kanmin Xue, Cristina Martinez-Fernandez de la Camara, Anika Nanda, Alexandra Davies, Laura J Wood, Anna Paola Salvetti, M Dominik Fischer, James W Aylward, Alun R Barnard,[...]. Nat Med 2020
21
Gene therapy for leber congenital amaurosis caused by RPE65 mutations: safety and efficacy in 15 children and adults followed up to 3 years.
Samuel G Jacobson, Artur V Cideciyan, Ramakrishna Ratnakaram, Elise Heon, Sharon B Schwartz, Alejandro J Roman, Marc C Peden, Tomas S Aleman, Sanford L Boye, Alexander Sumaroka,[...]. Arch Ophthalmol 2012
Samuel G Jacobson, Artur V Cideciyan, Ramakrishna Ratnakaram, Elise Heon, Sharon B Schwartz, Alejandro J Roman, Marc C Peden, Tomas S Aleman, Sanford L Boye, Alexander Sumaroka,[...]. Arch Ophthalmol 2012
20
The Spectrum of CHM Gene Mutations in Choroideremia and Their Relationship to Clinical Phenotype.
Matthew P Simunovic, Jasleen K Jolly, Kanmin Xue, Thomas L Edwards, Markus Groppe, Susan M Downes, Robert E MacLaren. Invest Ophthalmol Vis Sci 2016
Matthew P Simunovic, Jasleen K Jolly, Kanmin Xue, Thomas L Edwards, Markus Groppe, Susan M Downes, Robert E MacLaren. Invest Ophthalmol Vis Sci 2016
29
Measurement and Reproducibility of Preserved Ellipsoid Zone Area and Preserved Retinal Pigment Epithelium Area in Eyes With Choroideremia.
Amir H Hariri, Swetha B Velaga, Aniz Girach, Michael S Ip, Phuc V Le, Byron L Lam, M Dominik Fischer, Eeva-Marja Sankila, Mark E Pennesi, Frank G Holz,[...]. Am J Ophthalmol 2017
Amir H Hariri, Swetha B Velaga, Aniz Girach, Michael S Ip, Phuc V Le, Byron L Lam, M Dominik Fischer, Eeva-Marja Sankila, Mark E Pennesi, Frank G Holz,[...]. Am J Ophthalmol 2017
39
AAV8 Can Induce Innate and Adaptive Immune Response in the Primate Eye.
Felix F Reichel, Daniyar L Dauletbekov, Reinhild Klein, Tobias Peters, G Alex Ochakovski, Immanuel P Seitz, Barbara Wilhelm, Marius Ueffing, Martin Biel, Bernd Wissinger,[...]. Mol Ther 2017
Felix F Reichel, Daniyar L Dauletbekov, Reinhild Klein, Tobias Peters, G Alex Ochakovski, Immanuel P Seitz, Barbara Wilhelm, Marius Ueffing, Martin Biel, Bernd Wissinger,[...]. Mol Ther 2017
25
Safety and Long-Term Efficacy of AAV4 Gene Therapy in Patients with RPE65 Leber Congenital Amaurosis.
Guylène Le Meur, Pierre Lebranchu, Fanny Billaud, Oumeya Adjali, Sébastien Schmitt, Stéphane Bézieau, Yann Péréon, Romain Valabregue, Catherine Ivan, Christophe Darmon,[...]. Mol Ther 2018
Guylène Le Meur, Pierre Lebranchu, Fanny Billaud, Oumeya Adjali, Sébastien Schmitt, Stéphane Bézieau, Yann Péréon, Romain Valabregue, Catherine Ivan, Christophe Darmon,[...]. Mol Ther 2018
23
Treatment of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial.
William W Hauswirth, Tomas S Aleman, Shalesh Kaushal, Artur V Cideciyan, Sharon B Schwartz, Lili Wang, Thomas J Conlon, Sanford L Boye, Terence R Flotte, Barry J Byrne,[...]. Hum Gene Ther 2008
William W Hauswirth, Tomas S Aleman, Shalesh Kaushal, Artur V Cideciyan, Sharon B Schwartz, Lili Wang, Thomas J Conlon, Sanford L Boye, Terence R Flotte, Barry J Byrne,[...]. Hum Gene Ther 2008
16
Immune Response and Intraocular Inflammation in Patients With Leber Hereditary Optic Neuropathy Treated With Intravitreal Injection of Recombinant Adeno-Associated Virus 2 Carrying the ND4 Gene: A Secondary Analysis of a Phase 1/2 Clinical Trial.
Céline Bouquet, Catherine Vignal Clermont, Anne Galy, Serge Fitoussi, Laure Blouin, Marion R Munk, Sonia Valero, Sandrine Meunier, Barrett Katz, José Alain Sahel,[...]. JAMA Ophthalmol 2019
Céline Bouquet, Catherine Vignal Clermont, Anne Galy, Serge Fitoussi, Laure Blouin, Marion R Munk, Sonia Valero, Sandrine Meunier, Barrett Katz, José Alain Sahel,[...]. JAMA Ophthalmol 2019
30
High-resolution adaptive optics retinal imaging of cellular structure in choroideremia.
Jessica I W Morgan, Grace Han, Eva Klinman, William M Maguire, Daniel C Chung, Albert M Maguire, Jean Bennett. Invest Ophthalmol Vis Sci 2014
Jessica I W Morgan, Grace Han, Eva Klinman, William M Maguire, Daniel C Chung, Albert M Maguire, Jean Bennett. Invest Ophthalmol Vis Sci 2014
18
Results at 2 Years after Gene Therapy for RPE65-Deficient Leber Congenital Amaurosis and Severe Early-Childhood-Onset Retinal Dystrophy.
Richard G Weleber, Mark E Pennesi, David J Wilson, Shalesh Kaushal, Laura R Erker, Lauren Jensen, Maureen T McBride, Terence R Flotte, Margaret Humphries, Roberto Calcedo,[...]. Ophthalmology 2016
Richard G Weleber, Mark E Pennesi, David J Wilson, Shalesh Kaushal, Laura R Erker, Lauren Jensen, Maureen T McBride, Terence R Flotte, Margaret Humphries, Roberto Calcedo,[...]. Ophthalmology 2016
15
Gene Therapy for Leber Hereditary Optic Neuropathy: Low- and Medium-Dose Visual Results.
John Guy, William J Feuer, Janet L Davis, Vittorio Porciatti, Phillip J Gonzalez, Rajeshwari D Koilkonda, Huijun Yuan, William W Hauswirth, Byron L Lam. Ophthalmology 2017
John Guy, William J Feuer, Janet L Davis, Vittorio Porciatti, Phillip J Gonzalez, Rajeshwari D Koilkonda, Huijun Yuan, William W Hauswirth, Byron L Lam. Ophthalmology 2017
15
Safety and Vision Outcomes of Subretinal Gene Therapy Targeting Cone Photoreceptors in Achromatopsia: A Nonrandomized Controlled Trial.
M Dominik Fischer, Stylianos Michalakis, Barbara Wilhelm, Ditta Zobor, Regine Muehlfriedel, Susanne Kohl, Nicole Weisschuh, G Alex Ochakovski, Reinhild Klein, Christian Schoen,[...]. JAMA Ophthalmol 2020
M Dominik Fischer, Stylianos Michalakis, Barbara Wilhelm, Ditta Zobor, Regine Muehlfriedel, Susanne Kohl, Nicole Weisschuh, G Alex Ochakovski, Reinhild Klein, Christian Schoen,[...]. JAMA Ophthalmol 2020
25
Choroideremia: a review of general findings and pathogenesis.
Razek Georges Coussa, Elias I Traboulsi. Ophthalmic Genet 2012
Razek Georges Coussa, Elias I Traboulsi. Ophthalmic Genet 2012
16
Remodeling of the human retina in choroideremia: rab escort protein 1 (REP-1) mutations.
Samuel G Jacobson, Artur V Cideciyan, Alexander Sumaroka, Tomas S Aleman, Sharon B Schwartz, Elizabeth A M Windsor, Alejandro J Roman, Edwin M Stone, Ian M MacDonald. Invest Ophthalmol Vis Sci 2006
Samuel G Jacobson, Artur V Cideciyan, Alexander Sumaroka, Tomas S Aleman, Sharon B Schwartz, Elizabeth A M Windsor, Alejandro J Roman, Edwin M Stone, Ian M MacDonald. Invest Ophthalmol Vis Sci 2006
14
Visual Function and Central Retinal Structure in Choroideremia.
Elise Heon, Talal Alabduljalil, David B McGuigan III, Artur V Cideciyan, Shuning Li, Shiyi Chen, Samuel G Jacobson. Invest Ophthalmol Vis Sci 2016
Elise Heon, Talal Alabduljalil, David B McGuigan III, Artur V Cideciyan, Shuning Li, Shiyi Chen, Samuel G Jacobson. Invest Ophthalmol Vis Sci 2016
26
Evaluation of Dose and Safety of AAV7m8 and AAV8BP2 in the Non-Human Primate Retina.
Pavitra S Ramachandran, Vivian Lee, Zhangyong Wei, Ji Yun Song, Giulia Casal, Therese Cronin, Keirnan Willett, Rachel Huckfeldt, Jessica I W Morgan, Tomas S Aleman,[...]. Hum Gene Ther 2017
Pavitra S Ramachandran, Vivian Lee, Zhangyong Wei, Ji Yun Song, Giulia Casal, Therese Cronin, Keirnan Willett, Rachel Huckfeldt, Jessica I W Morgan, Tomas S Aleman,[...]. Hum Gene Ther 2017
17
Clinical and Genetic Features of Choroideremia in Childhood.
Kamron N Khan, Farrah Islam, Anthony T Moore, Michel Michaelides. Ophthalmology 2016
Kamron N Khan, Farrah Islam, Anthony T Moore, Michel Michaelides. Ophthalmology 2016
31
In vivo-directed evolution of a new adeno-associated virus for therapeutic outer retinal gene delivery from the vitreous.
Deniz Dalkara, Leah C Byrne, Ryan R Klimczak, Meike Visel, Lu Yin, William H Merigan, John G Flannery, David V Schaffer. Sci Transl Med 2013
Deniz Dalkara, Leah C Byrne, Ryan R Klimczak, Meike Visel, Lu Yin, William H Merigan, John G Flannery, David V Schaffer. Sci Transl Med 2013
14
Gene Therapy for Leber Hereditary Optic Neuropathy: Initial Results.
William J Feuer, Joyce C Schiffman, Janet L Davis, Vittorio Porciatti, Phillip Gonzalez, Rajeshwari D Koilkonda, Huijun Yuan, Anil Lalwani, Byron L Lam, John Guy. Ophthalmology 2016
William J Feuer, Joyce C Schiffman, Janet L Davis, Vittorio Porciatti, Phillip Gonzalez, Rajeshwari D Koilkonda, Huijun Yuan, Anil Lalwani, Byron L Lam, John Guy. Ophthalmology 2016
13
Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement.
Artur V Cideciyan, Samuel G Jacobson, William A Beltran, Alexander Sumaroka, Malgorzata Swider, Simone Iwabe, Alejandro J Roman, Melani B Olivares, Sharon B Schwartz, András M Komáromy,[...]. Proc Natl Acad Sci U S A 2013
Artur V Cideciyan, Samuel G Jacobson, William A Beltran, Alexander Sumaroka, Malgorzata Swider, Simone Iwabe, Alejandro J Roman, Melani B Olivares, Sharon B Schwartz, András M Komáromy,[...]. Proc Natl Acad Sci U S A 2013
13
Functional expression of Rab escort protein 1 following AAV2-mediated gene delivery in the retina of choroideremia mice and human cells ex vivo.
Tanya Tolmachova, Oleg E Tolmachov, Alun R Barnard, Samantha R de Silva, Daniel M Lipinski, Nathan J Walker, Robert E Maclaren, Miguel C Seabra. J Mol Med (Berl) 2013
Tanya Tolmachova, Oleg E Tolmachov, Alun R Barnard, Samantha R de Silva, Daniel M Lipinski, Nathan J Walker, Robert E Maclaren, Miguel C Seabra. J Mol Med (Berl) 2013
20
Retinal Degeneration in Choroideremia follows an Exponential Decay Function.
James W Aylward, Kanmin Xue, Maria I Patrício, Jasleen K Jolly, Jonathan C Wood, Jonathan Brett, Kirti M Jasani, Robert E MacLaren. Ophthalmology 2018
James W Aylward, Kanmin Xue, Maria I Patrício, Jasleen K Jolly, Jonathan C Wood, Jonathan Brett, Kirti M Jasani, Robert E MacLaren. Ophthalmology 2018
56
Correlation of Optical Coherence Tomography and Autofluorescence in the Outer Retina and Choroid of Patients With Choroideremia.
Kanmin Xue, Marta Oldani, Jasleen K Jolly, Thomas L Edwards, Markus Groppe, Susan M Downes, Robert E MacLaren. Invest Ophthalmol Vis Sci 2016
Kanmin Xue, Marta Oldani, Jasleen K Jolly, Thomas L Edwards, Markus Groppe, Susan M Downes, Robert E MacLaren. Invest Ophthalmol Vis Sci 2016
22
A Qualitative and Quantitative Assessment of Fundus Autofluorescence Patterns in Patients With Choroideremia.
Jasleen K Jolly, Thomas L Edwards, Jonathan Moules, Markus Groppe, Susan M Downes, Robert E MacLaren. Invest Ophthalmol Vis Sci 2016
Jasleen K Jolly, Thomas L Edwards, Jonathan Moules, Markus Groppe, Susan M Downes, Robert E MacLaren. Invest Ophthalmol Vis Sci 2016
26
Correlation of retinal structure and function in choroideremia carriers.
Thomas L Edwards, Markus Groppe, Jasleen K Jolly, Susan M Downes, Robert E MacLaren. Ophthalmology 2015
Thomas L Edwards, Markus Groppe, Jasleen K Jolly, Susan M Downes, Robert E MacLaren. Ophthalmology 2015
35
Intraocular route of AAV2 vector administration defines humoral immune response and therapeutic potential.
Qiuhong Li, Rehae Miller, Ping-Yang Han, Jijing Pang, Astra Dinculescu, Vince Chiodo, William W Hauswirth. Mol Vis 2008
Qiuhong Li, Rehae Miller, Ping-Yang Han, Jijing Pang, Astra Dinculescu, Vince Chiodo, William W Hauswirth. Mol Vis 2008
13
Improvement and decline in vision with gene therapy in childhood blindness.
Samuel G Jacobson, Artur V Cideciyan, Alejandro J Roman, Alexander Sumaroka, Sharon B Schwartz, Elise Heon, William W Hauswirth. N Engl J Med 2015
Samuel G Jacobson, Artur V Cideciyan, Alejandro J Roman, Alexander Sumaroka, Sharon B Schwartz, Elise Heon, William W Hauswirth. N Engl J Med 2015
13
Effect of an intravitreal antisense oligonucleotide on vision in Leber congenital amaurosis due to a photoreceptor cilium defect.
Artur V Cideciyan, Samuel G Jacobson, Arlene V Drack, Allen C Ho, Jason Charng, Alexandra V Garafalo, Alejandro J Roman, Alexander Sumaroka, Ian C Han, Maria D Hochstedler,[...]. Nat Med 2019
Artur V Cideciyan, Samuel G Jacobson, Arlene V Drack, Allen C Ho, Jason Charng, Alexandra V Garafalo, Alejandro J Roman, Alexander Sumaroka, Ian C Han, Maria D Hochstedler,[...]. Nat Med 2019
13
Humoral Immune Response After Intravitreal But Not After Subretinal AAV8 in Primates and Patients.
Felix F Reichel, Tobias Peters, Barbara Wilhelm, Martin Biel, Marius Ueffing, Bernd Wissinger, Karl U Bartz-Schmidt, Reinhild Klein, Stylianos Michalakis, M Dominik Fischer. Invest Ophthalmol Vis Sci 2018
Felix F Reichel, Tobias Peters, Barbara Wilhelm, Martin Biel, Marius Ueffing, Bernd Wissinger, Karl U Bartz-Schmidt, Reinhild Klein, Stylianos Michalakis, M Dominik Fischer. Invest Ophthalmol Vis Sci 2018
27
Efficacy and Safety of rAAV2-ND4 Treatment for Leber's Hereditary Optic Neuropathy.
Xing Wan, Han Pei, Min-jian Zhao, Shuo Yang, Wei-kun Hu, Heng He, Si-qi Ma, Ge Zhang, Xiao-yan Dong, Chen Chen,[...]. Sci Rep 2016
Xing Wan, Han Pei, Min-jian Zhao, Shuo Yang, Wei-kun Hu, Heng He, Si-qi Ma, Ge Zhang, Xiao-yan Dong, Chen Chen,[...]. Sci Rep 2016
12
Co-cited is the co-citation frequency, indicating how many articles cite the article together with the query article. Similarity is the co-citation as percentage of the times cited of the query article or the article in the search results, whichever is the lowest. These numbers are calculated for the last 100 citations when articles are cited more than 100 times.