Ivana Trapani, Alberto Auricchio. Trends Mol Med 2018
Times Cited: 61
Times Cited: 61
Times Cited
Times Co-cited
Similarity
Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial.
Stephen Russell, Jean Bennett, Jennifer A Wellman, Daniel C Chung, Zi-Fan Yu, Amy Tillman, Janet Wittes, Julie Pappas, Okan Elci, Sarah McCague,[...]. Lancet 2017
Stephen Russell, Jean Bennett, Jennifer A Wellman, Daniel C Chung, Zi-Fan Yu, Amy Tillman, Janet Wittes, Julie Pappas, Okan Elci, Sarah McCague,[...]. Lancet 2017
37
In vivo-directed evolution of a new adeno-associated virus for therapeutic outer retinal gene delivery from the vitreous.
Deniz Dalkara, Leah C Byrne, Ryan R Klimczak, Meike Visel, Lu Yin, William H Merigan, John G Flannery, David V Schaffer. Sci Transl Med 2013
Deniz Dalkara, Leah C Byrne, Ryan R Klimczak, Meike Visel, Lu Yin, William H Merigan, John G Flannery, David V Schaffer. Sci Transl Med 2013
24
Effect of gene therapy on visual function in Leber's congenital amaurosis.
James W B Bainbridge, Alexander J Smith, Susie S Barker, Scott Robbie, Robert Henderson, Kamaljit Balaggan, Ananth Viswanathan, Graham E Holder, Andrew Stockman, Nick Tyler,[...]. N Engl J Med 2008
James W B Bainbridge, Alexander J Smith, Susie S Barker, Scott Robbie, Robert Henderson, Kamaljit Balaggan, Ananth Viswanathan, Graham E Holder, Andrew Stockman, Nick Tyler,[...]. N Engl J Med 2008
22
Safety and efficacy of gene transfer for Leber's congenital amaurosis.
Albert M Maguire, Francesca Simonelli, Eric A Pierce, Edward N Pugh, Federico Mingozzi, Jeannette Bennicelli, Sandro Banfi, Kathleen A Marshall, Francesco Testa, Enrico M Surace,[...]. N Engl J Med 2008
Albert M Maguire, Francesca Simonelli, Eric A Pierce, Edward N Pugh, Federico Mingozzi, Jeannette Bennicelli, Sandro Banfi, Kathleen A Marshall, Francesco Testa, Enrico M Surace,[...]. N Engl J Med 2008
18
Gene therapy for leber congenital amaurosis caused by RPE65 mutations: safety and efficacy in 15 children and adults followed up to 3 years.
Samuel G Jacobson, Artur V Cideciyan, Ramakrishna Ratnakaram, Elise Heon, Sharon B Schwartz, Alejandro J Roman, Marc C Peden, Tomas S Aleman, Sanford L Boye, Alexander Sumaroka,[...]. Arch Ophthalmol 2012
Samuel G Jacobson, Artur V Cideciyan, Ramakrishna Ratnakaram, Elise Heon, Sharon B Schwartz, Alejandro J Roman, Marc C Peden, Tomas S Aleman, Sanford L Boye, Alexander Sumaroka,[...]. Arch Ophthalmol 2012
16
Effect of an intravitreal antisense oligonucleotide on vision in Leber congenital amaurosis due to a photoreceptor cilium defect.
Artur V Cideciyan, Samuel G Jacobson, Arlene V Drack, Allen C Ho, Jason Charng, Alexandra V Garafalo, Alejandro J Roman, Alexander Sumaroka, Ian C Han, Maria D Hochstedler,[...]. Nat Med 2019
Artur V Cideciyan, Samuel G Jacobson, Arlene V Drack, Allen C Ho, Jason Charng, Alexandra V Garafalo, Alejandro J Roman, Alexander Sumaroka, Ian C Han, Maria D Hochstedler,[...]. Nat Med 2019
16
Development of a gene-editing approach to restore vision loss in Leber congenital amaurosis type 10.
Morgan L Maeder, Michael Stefanidakis, Christopher J Wilson, Reshica Baral, Luis Alberto Barrera, George S Bounoutas, David Bumcrot, Hoson Chao, Dawn M Ciulla, Jennifer A DaSilva,[...]. Nat Med 2019
Morgan L Maeder, Michael Stefanidakis, Christopher J Wilson, Reshica Baral, Luis Alberto Barrera, George S Bounoutas, David Bumcrot, Hoson Chao, Dawn M Ciulla, Jennifer A DaSilva,[...]. Nat Med 2019
16
Treatment of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial.
William W Hauswirth, Tomas S Aleman, Shalesh Kaushal, Artur V Cideciyan, Sharon B Schwartz, Lili Wang, Thomas J Conlon, Sanford L Boye, Terence R Flotte, Barry J Byrne,[...]. Hum Gene Ther 2008
William W Hauswirth, Tomas S Aleman, Shalesh Kaushal, Artur V Cideciyan, Sharon B Schwartz, Lili Wang, Thomas J Conlon, Sanford L Boye, Terence R Flotte, Barry J Byrne,[...]. Hum Gene Ther 2008
14
Effective delivery of large genes to the retina by dual AAV vectors.
Ivana Trapani, Pasqualina Colella, Andrea Sommella, Carolina Iodice, Giulia Cesi, Sonia de Simone, Elena Marrocco, Settimio Rossi, Massimo Giunti, Arpad Palfi,[...]. EMBO Mol Med 2014
Ivana Trapani, Pasqualina Colella, Andrea Sommella, Carolina Iodice, Giulia Cesi, Sonia de Simone, Elena Marrocco, Settimio Rossi, Massimo Giunti, Arpad Palfi,[...]. EMBO Mol Med 2014
14
Long-term effect of gene therapy on Leber's congenital amaurosis.
James W B Bainbridge, Manjit S Mehat, Venki Sundaram, Scott J Robbie, Susie E Barker, Caterina Ripamonti, Anastasios Georgiadis, Freya M Mowat, Stuart G Beattie, Peter J Gardner,[...]. N Engl J Med 2015
James W B Bainbridge, Manjit S Mehat, Venki Sundaram, Scott J Robbie, Susie E Barker, Caterina Ripamonti, Anastasios Georgiadis, Freya M Mowat, Stuart G Beattie, Peter J Gardner,[...]. N Engl J Med 2015
14
Safety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutations: a follow-on phase 1 trial.
Jean Bennett, Jennifer Wellman, Kathleen A Marshall, Sarah McCague, Manzar Ashtari, Julie DiStefano-Pappas, Okan U Elci, Daniel C Chung, Junwei Sun, J Fraser Wright,[...]. Lancet 2016
Jean Bennett, Jennifer Wellman, Kathleen A Marshall, Sarah McCague, Manzar Ashtari, Julie DiStefano-Pappas, Okan U Elci, Daniel C Chung, Junwei Sun, J Fraser Wright,[...]. Lancet 2016
14
In Silico Reconstruction of the Viral Evolutionary Lineage Yields a Potent Gene Therapy Vector.
Eric Zinn, Simon Pacouret, Vadim Khaychuk, Heikki T Turunen, Livia S Carvalho, Eva Andres-Mateos, Samiksha Shah, Rajani Shelke, Anna C Maurer, Eva Plovie,[...]. Cell Rep 2015
Eric Zinn, Simon Pacouret, Vadim Khaychuk, Heikki T Turunen, Livia S Carvalho, Eva Andres-Mateos, Samiksha Shah, Rajani Shelke, Anna C Maurer, Eva Plovie,[...]. Cell Rep 2015
13
Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery.
Catherine Cukras, Henry E Wiley, Brett G Jeffrey, H Nida Sen, Amy Turriff, Yong Zeng, Camasamudram Vijayasarathy, Dario Marangoni, Lucia Ziccardi, Sten Kjellstrom,[...]. Mol Ther 2018
Catherine Cukras, Henry E Wiley, Brett G Jeffrey, H Nida Sen, Amy Turriff, Yong Zeng, Camasamudram Vijayasarathy, Dario Marangoni, Lucia Ziccardi, Sten Kjellstrom,[...]. Mol Ther 2018
13
Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement.
Artur V Cideciyan, Samuel G Jacobson, William A Beltran, Alexander Sumaroka, Malgorzata Swider, Simone Iwabe, Alejandro J Roman, Melani B Olivares, Sharon B Schwartz, András M Komáromy,[...]. Proc Natl Acad Sci U S A 2013
Artur V Cideciyan, Samuel G Jacobson, William A Beltran, Alexander Sumaroka, Malgorzata Swider, Simone Iwabe, Alejandro J Roman, Melani B Olivares, Sharon B Schwartz, András M Komáromy,[...]. Proc Natl Acad Sci U S A 2013
13
Vector platforms for gene therapy of inherited retinopathies.
Ivana Trapani, Agostina Puppo, Alberto Auricchio. Prog Retin Eye Res 2014
Ivana Trapani, Agostina Puppo, Alberto Auricchio. Prog Retin Eye Res 2014
11
Splice-Modulating Oligonucleotide QR-110 Restores CEP290 mRNA and Function in Human c.2991+1655A>G LCA10 Models.
Kalyan Dulla, Monica Aguila, Amelia Lane, Katarina Jovanovic, David A Parfitt, Iris Schulkens, Hee Lam Chan, Iris Schmidt, Wouter Beumer, Lars Vorthoren,[...]. Mol Ther Nucleic Acids 2018
Kalyan Dulla, Monica Aguila, Amelia Lane, Katarina Jovanovic, David A Parfitt, Iris Schulkens, Hee Lam Chan, Iris Schmidt, Wouter Beumer, Lars Vorthoren,[...]. Mol Ther Nucleic Acids 2018
11
Improvement and decline in vision with gene therapy in childhood blindness.
Samuel G Jacobson, Artur V Cideciyan, Alejandro J Roman, Alexander Sumaroka, Sharon B Schwartz, Elise Heon, William W Hauswirth. N Engl J Med 2015
Samuel G Jacobson, Artur V Cideciyan, Alejandro J Roman, Alexander Sumaroka, Sharon B Schwartz, Elise Heon, William W Hauswirth. N Engl J Med 2015
11
Three-year follow-up after unilateral subretinal delivery of adeno-associated virus in patients with Leber congenital Amaurosis type 2.
Francesco Testa, Albert M Maguire, Settimio Rossi, Eric A Pierce, Paolo Melillo, Kathleen Marshall, Sandro Banfi, Enrico M Surace, Junwei Sun, Carmela Acerra,[...]. Ophthalmology 2013
Francesco Testa, Albert M Maguire, Settimio Rossi, Eric A Pierce, Paolo Melillo, Kathleen Marshall, Sandro Banfi, Enrico M Surace, Junwei Sun, Carmela Acerra,[...]. Ophthalmology 2013
11
Choroideremia Gene Therapy Phase 2 Clinical Trial: 24-Month Results.
Byron L Lam, Janet L Davis, Ninel Z Gregori, Robert E MacLaren, Aniz Girach, Jennifer D Verriotto, Belen Rodriguez, Potyra R Rosa, Xiaojun Zhang, William J Feuer. Am J Ophthalmol 2019
Byron L Lam, Janet L Davis, Ninel Z Gregori, Robert E MacLaren, Aniz Girach, Jennifer D Verriotto, Belen Rodriguez, Potyra R Rosa, Xiaojun Zhang, William J Feuer. Am J Ophthalmol 2019
11
Progress in treating inherited retinal diseases: Early subretinal gene therapy clinical trials and candidates for future initiatives.
Alexandra V Garafalo, Artur V Cideciyan, Elise Héon, Rebecca Sheplock, Alexander Pearson, Caberry WeiYang Yu, Alexander Sumaroka, Gustavo D Aguirre, Samuel G Jacobson. Prog Retin Eye Res 2020
Alexandra V Garafalo, Artur V Cideciyan, Elise Héon, Rebecca Sheplock, Alexander Pearson, Caberry WeiYang Yu, Alexander Sumaroka, Gustavo D Aguirre, Samuel G Jacobson. Prog Retin Eye Res 2020
11
Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR.
Jasmina Cehajic-Kapetanovic, Kanmin Xue, Cristina Martinez-Fernandez de la Camara, Anika Nanda, Alexandra Davies, Laura J Wood, Anna Paola Salvetti, M Dominik Fischer, James W Aylward, Alun R Barnard,[...]. Nat Med 2020
Jasmina Cehajic-Kapetanovic, Kanmin Xue, Cristina Martinez-Fernandez de la Camara, Anika Nanda, Alexandra Davies, Laura J Wood, Anna Paola Salvetti, M Dominik Fischer, James W Aylward, Alun R Barnard,[...]. Nat Med 2020
11
Noninvasive gene delivery to foveal cones for vision restoration.
Hanen Khabou, Marcela Garita-Hernandez, Antoine Chaffiol, Sacha Reichman, Céline Jaillard, Elena Brazhnikova, Stéphane Bertin, Valérie Forster, Mélissa Desrosiers, Céline Winckler,[...]. JCI Insight 2018
Hanen Khabou, Marcela Garita-Hernandez, Antoine Chaffiol, Sacha Reichman, Céline Jaillard, Elena Brazhnikova, Stéphane Bertin, Valérie Forster, Mélissa Desrosiers, Céline Winckler,[...]. JCI Insight 2018
9
High-efficiency transduction of the mouse retina by tyrosine-mutant AAV serotype vectors.
Hilda Petrs-Silva, Astra Dinculescu, Qiuhong Li, Seok-Hong Min, Vince Chiodo, Ji-Jing Pang, Li Zhong, Sergei Zolotukhin, Arun Srivastava, Alfred S Lewin,[...]. Mol Ther 2009
Hilda Petrs-Silva, Astra Dinculescu, Qiuhong Li, Seok-Hong Min, Vince Chiodo, Ji-Jing Pang, Li Zhong, Sergei Zolotukhin, Arun Srivastava, Alfred S Lewin,[...]. Mol Ther 2009
9
Adeno-associated virus vector as a platform for gene therapy delivery.
Dan Wang, Phillip W L Tai, Guangping Gao. Nat Rev Drug Discov 2019
Dan Wang, Phillip W L Tai, Guangping Gao. Nat Rev Drug Discov 2019
9
25
Dual adeno-associated virus vectors result in efficient in vitro and in vivo expression of an oversized gene, MYO7A.
Frank M Dyka, Sanford L Boye, Vince A Chiodo, William W Hauswirth, Shannon E Boye. Hum Gene Ther Methods 2014
Frank M Dyka, Sanford L Boye, Vince A Chiodo, William W Hauswirth, Shannon E Boye. Hum Gene Ther Methods 2014
9
Triple Vectors Expand AAV Transfer Capacity in the Retina.
Andrea Maddalena, Patrizia Tornabene, Paola Tiberi, Renato Minopoli, Anna Manfredi, Margherita Mutarelli, Settimio Rossi, Francesca Simonelli, Jurgen K Naggert, Davide Cacchiarelli,[...]. Mol Ther 2018
Andrea Maddalena, Patrizia Tornabene, Paola Tiberi, Renato Minopoli, Anna Manfredi, Margherita Mutarelli, Settimio Rossi, Francesca Simonelli, Jurgen K Naggert, Davide Cacchiarelli,[...]. Mol Ther 2018
10
In vivo genome editing via CRISPR/Cas9 mediated homology-independent targeted integration.
Keiichiro Suzuki, Yuji Tsunekawa, Reyna Hernandez-Benitez, Jun Wu, Jie Zhu, Euiseok J Kim, Fumiyuki Hatanaka, Mako Yamamoto, Toshikazu Araoka, Zhe Li,[...]. Nature 2016
Keiichiro Suzuki, Yuji Tsunekawa, Reyna Hernandez-Benitez, Jun Wu, Jie Zhu, Euiseok J Kim, Fumiyuki Hatanaka, Mako Yamamoto, Toshikazu Araoka, Zhe Li,[...]. Nature 2016
9
Treatment of retinitis pigmentosa due to MERTK mutations by ocular subretinal injection of adeno-associated virus gene vector: results of a phase I trial.
Nicola G Ghazi, Emad B Abboud, Sawsan R Nowilaty, Hisham Alkuraya, Abdulrahman Alhommadi, Huimin Cai, Rui Hou, Wen-Tao Deng, Sanford L Boye, Abdulrahman Almaghamsi,[...]. Hum Genet 2016
Nicola G Ghazi, Emad B Abboud, Sawsan R Nowilaty, Hisham Alkuraya, Abdulrahman Alhommadi, Huimin Cai, Rui Hou, Wen-Tao Deng, Sanford L Boye, Abdulrahman Almaghamsi,[...]. Hum Genet 2016
9
Evaluation of Dose and Safety of AAV7m8 and AAV8BP2 in the Non-Human Primate Retina.
Pavitra S Ramachandran, Vivian Lee, Zhangyong Wei, Ji Yun Song, Giulia Casal, Therese Cronin, Keirnan Willett, Rachel Huckfeldt, Jessica I W Morgan, Tomas S Aleman,[...]. Hum Gene Ther 2017
Pavitra S Ramachandran, Vivian Lee, Zhangyong Wei, Ji Yun Song, Giulia Casal, Therese Cronin, Keirnan Willett, Rachel Huckfeldt, Jessica I W Morgan, Tomas S Aleman,[...]. Hum Gene Ther 2017
9
Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial.
Robert E MacLaren, Markus Groppe, Alun R Barnard, Charles L Cottriall, Tanya Tolmachova, Len Seymour, K Reed Clark, Matthew J During, Frans P M Cremers, Graeme C M Black,[...]. Lancet 2014
Robert E MacLaren, Markus Groppe, Alun R Barnard, Charles L Cottriall, Tanya Tolmachova, Len Seymour, K Reed Clark, Matthew J During, Frans P M Cremers, Graeme C M Black,[...]. Lancet 2014
9
Insight into the mechanisms of enhanced retinal transduction by the engineered AAV2 capsid variant -7m8.
Hanen Khabou, Mélissa Desrosiers, Céline Winckler, Stéphane Fouquet, Gwenaëlle Auregan, Alexis-Pierre Bemelmans, José-Alain Sahel, Deniz Dalkara. Biotechnol Bioeng 2016
Hanen Khabou, Mélissa Desrosiers, Céline Winckler, Stéphane Fouquet, Gwenaëlle Auregan, Alexis-Pierre Bemelmans, José-Alain Sahel, Deniz Dalkara. Biotechnol Bioeng 2016
14
Effect of genome size on AAV vector packaging.
Zhijian Wu, Hongyan Yang, Peter Colosi. Mol Ther 2010
Zhijian Wu, Hongyan Yang, Peter Colosi. Mol Ther 2010
8
Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors.
Mariacarmela Allocca, Claudio Mussolino, Maria Garcia-Hoyos, Daniela Sanges, Carolina Iodice, Marco Petrillo, Luk H Vandenberghe, James M Wilson, Valeria Marigo, Enrico M Surace,[...]. J Virol 2007
Mariacarmela Allocca, Claudio Mussolino, Maria Garcia-Hoyos, Daniela Sanges, Carolina Iodice, Marco Petrillo, Luk H Vandenberghe, James M Wilson, Valeria Marigo, Enrico M Surace,[...]. J Virol 2007
8
Improved Intravitreal AAV-Mediated Inner Retinal Gene Transduction after Surgical Internal Limiting Membrane Peeling in Cynomolgus Monkeys.
Kazuhisa Takahashi, Tsutomu Igarashi, Koichi Miyake, Maika Kobayashi, Chiemi Yaguchi, Osamu Iijima, Yoshiyuki Yamazaki, Yuko Katakai, Noriko Miyake, Shuhei Kameya,[...]. Mol Ther 2017
Kazuhisa Takahashi, Tsutomu Igarashi, Koichi Miyake, Maika Kobayashi, Chiemi Yaguchi, Osamu Iijima, Yoshiyuki Yamazaki, Yuko Katakai, Noriko Miyake, Shuhei Kameya,[...]. Mol Ther 2017
10
Efficient gene delivery to the cone-enriched pig retina by dual AAV vectors.
P Colella, I Trapani, G Cesi, A Sommella, A Manfredi, A Puppo, C Iodice, S Rossi, F Simonelli, M Giunti,[...]. Gene Ther 2014
P Colella, I Trapani, G Cesi, A Sommella, A Manfredi, A Puppo, C Iodice, S Rossi, F Simonelli, M Giunti,[...]. Gene Ther 2014
8
An AAV Dual Vector Strategy Ameliorates the Stargardt Phenotype in Adult Abca4-/- Mice.
Michelle E McClements, Alun R Barnard, Mandeep S Singh, Peter Charbel Issa, Zhichun Jiang, Roxana A Radu, Robert E MacLaren. Hum Gene Ther 2019
Michelle E McClements, Alun R Barnard, Mandeep S Singh, Peter Charbel Issa, Zhichun Jiang, Roxana A Radu, Robert E MacLaren. Hum Gene Ther 2019
11
Gene therapy restores vision in a canine model of childhood blindness.
G M Acland, G D Aguirre, J Ray, Q Zhang, T S Aleman, A V Cideciyan, S E Pearce-Kelling, V Anand, Y Zeng, A M Maguire,[...]. Nat Genet 2001
G M Acland, G D Aguirre, J Ray, Q Zhang, T S Aleman, A V Cideciyan, S E Pearce-Kelling, V Anand, Y Zeng, A M Maguire,[...]. Nat Genet 2001
8
Leber congenital amaurosis: genes, proteins and disease mechanisms.
Anneke I den Hollander, Ronald Roepman, Robert K Koenekoop, Frans P M Cremers. Prog Retin Eye Res 2008
Anneke I den Hollander, Ronald Roepman, Robert K Koenekoop, Frans P M Cremers. Prog Retin Eye Res 2008
8
Clinically Focused Molecular Investigation of 1000 Consecutive Families with Inherited Retinal Disease.
Edwin M Stone, Jeaneen L Andorf, S Scott Whitmore, Adam P DeLuca, Joseph C Giacalone, Luan M Streb, Terry A Braun, Robert F Mullins, Todd E Scheetz, Val C Sheffield,[...]. Ophthalmology 2017
Edwin M Stone, Jeaneen L Andorf, S Scott Whitmore, Adam P DeLuca, Joseph C Giacalone, Luan M Streb, Terry A Braun, Robert F Mullins, Todd E Scheetz, Val C Sheffield,[...]. Ophthalmology 2017
8
CRISPR/Cas9-Mediated Genome Editing as a Therapeutic Approach for Leber Congenital Amaurosis 10.
Guo-Xiang Ruan, Elizabeth Barry, Dan Yu, Michael Lukason, Seng H Cheng, Abraham Scaria. Mol Ther 2017
Guo-Xiang Ruan, Elizabeth Barry, Dan Yu, Michael Lukason, Seng H Cheng, Abraham Scaria. Mol Ther 2017
8
Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics.
Artur V Cideciyan, Tomas S Aleman, Sanford L Boye, Sharon B Schwartz, Shalesh Kaushal, Alejandro J Roman, Ji-Jing Pang, Alexander Sumaroka, Elizabeth A M Windsor, James M Wilson,[...]. Proc Natl Acad Sci U S A 2008
Artur V Cideciyan, Tomas S Aleman, Sanford L Boye, Sharon B Schwartz, Shalesh Kaushal, Alejandro J Roman, Ji-Jing Pang, Alexander Sumaroka, Elizabeth A M Windsor, James M Wilson,[...]. Proc Natl Acad Sci U S A 2008
8
Adeno-associated Virus (AAV) Dual Vector Strategies for Gene Therapy Encoding Large Transgenes.
Michelle E McClements, Robert E MacLaren. Yale J Biol Med 2017
Michelle E McClements, Robert E MacLaren. Yale J Biol Med 2017
12
DNA nanoparticles are safe and nontoxic in non-human primate eyes.
Ryan A Kelley, Shannon M Conley, Rasha Makkia, Jamie N Watson, Zongchao Han, Mark J Cooper, Muna I Naash. Int J Nanomedicine 2018
Ryan A Kelley, Shannon M Conley, Rasha Makkia, Jamie N Watson, Zongchao Han, Mark J Cooper, Muna I Naash. Int J Nanomedicine 2018
31
Tyrosine capsid-mutant AAV vectors for gene delivery to the canine retina from a subretinal or intravitreal approach.
F M Mowat, K R Gornik, A Dinculescu, S L Boye, W W Hauswirth, S M Petersen-Jones, J T Bartoe. Gene Ther 2014
F M Mowat, K R Gornik, A Dinculescu, S L Boye, W W Hauswirth, S M Petersen-Jones, J T Bartoe. Gene Ther 2014
8
Two-Year Results After AAV2-Mediated Gene Therapy for Choroideremia: The Alberta Experience.
Ioannis S Dimopoulos, Stephanie C Hoang, Alina Radziwon, Natalia M Binczyk, Miguel C Seabra, Robert E MacLaren, Rizwan Somani, Matthew T S Tennant, Ian M MacDonald. Am J Ophthalmol 2018
Ioannis S Dimopoulos, Stephanie C Hoang, Alina Radziwon, Natalia M Binczyk, Miguel C Seabra, Robert E MacLaren, Rizwan Somani, Matthew T S Tennant, Ian M MacDonald. Am J Ophthalmol 2018
8
A novel adeno-associated viral variant for efficient and selective intravitreal transduction of rat Müller cells.
Ryan R Klimczak, James T Koerber, Deniz Dalkara, John G Flannery, David V Schaffer. PLoS One 2009
Ryan R Klimczak, James T Koerber, Deniz Dalkara, John G Flannery, David V Schaffer. PLoS One 2009
8
Inherited Retinal Degenerations: Current Landscape and Knowledge Gaps.
Jacque L Duncan, Eric A Pierce, Amy M Laster, Stephen P Daiger, David G Birch, John D Ash, Alessandro Iannaccone, John G Flannery, José A Sahel, Donald J Zack,[...]. Transl Vis Sci Technol 2018
Jacque L Duncan, Eric A Pierce, Amy M Laster, Stephen P Daiger, David G Birch, John D Ash, Alessandro Iannaccone, John G Flannery, José A Sahel, Donald J Zack,[...]. Transl Vis Sci Technol 2018
8
Gene Therapy in Retinal Dystrophies.
Lucia Ziccardi, Viviana Cordeddu, Lucia Gaddini, Andrea Matteucci, Mariacristina Parravano, Fiorella Malchiodi-Albedi, Monica Varano. Int J Mol Sci 2019
Lucia Ziccardi, Viviana Cordeddu, Lucia Gaddini, Andrea Matteucci, Mariacristina Parravano, Fiorella Malchiodi-Albedi, Monica Varano. Int J Mol Sci 2019
11
Co-cited is the co-citation frequency, indicating how many articles cite the article together with the query article. Similarity is the co-citation as percentage of the times cited of the query article or the article in the search results, whichever is the lowest. These numbers are calculated for the last 100 citations when articles are cited more than 100 times.