A citation-based method for searching scientific literature

Da Sun, Rebecca M Schur, Avery E Sears, Song-Qi Gao, Amita Vaidya, Wenyu Sun, Akiko Maeda, Timothy Kern, Krzysztof Palczewski, Zheng-Rong Lu. Mol Ther 2020
Times Cited: 14







List of co-cited articles
249 articles co-cited >1



Times Cited
  Times     Co-cited
Similarity


Targeted Multifunctional Lipid ECO Plasmid DNA Nanoparticles as Efficient Non-viral Gene Therapy for Leber's Congenital Amaurosis.
Da Sun, Bhubanananda Sahu, Songqi Gao, Rebecca M Schur, Amita M Vaidya, Akiko Maeda, Krzysztof Palczewski, Zheng-Rong Lu. Mol Ther Nucleic Acids 2017
23
42

An AAV Dual Vector Strategy Ameliorates the Stargardt Phenotype in Adult Abca4-/- Mice.
Michelle E McClements, Alun R Barnard, Mandeep S Singh, Peter Charbel Issa, Zhichun Jiang, Roxana A Radu, Robert E MacLaren. Hum Gene Ther 2019
38
42

Design and evaluation of new pH-sensitive amphiphilic cationic lipids for siRNA delivery.
Anthony S Malamas, Maneesh Gujrati, China M Kummitha, Rongzuo Xu, Zheng-Rong Lu. J Control Release 2013
63
35

Long-term effect of gene therapy on Leber's congenital amaurosis.
James W B Bainbridge, Manjit S Mehat, Venki Sundaram, Scott J Robbie, Susie E Barker, Caterina Ripamonti, Anastasios Georgiadis, Freya M Mowat, Stuart G Beattie, Peter J Gardner,[...]. N Engl J Med 2015
429
35

A photoreceptor cell-specific ATP-binding transporter gene (ABCR) is mutated in recessive Stargardt macular dystrophy.
R Allikmets, N Singh, H Sun, N F Shroyer, A Hutchinson, A Chidambaram, B Gerrard, L Baird, D Stauffer, A Peiffer,[...]. Nat Genet 1997
966
35

DNA nanoparticle-mediated ABCA4 delivery rescues Stargardt dystrophy in mice.
Zongchao Han, Shannon M Conley, Rasha S Makkia, Mark J Cooper, Muna I Naash. J Clin Invest 2012
98
35

Dual ABCA4-AAV Vector Treatment Reduces Pathogenic Retinal A2E Accumulation in a Mouse Model of Autosomal Recessive Stargardt Disease.
Frank M Dyka, Laurie L Molday, Vince A Chiodo, Robert S Molday, William W Hauswirth. Hum Gene Ther 2019
16
35

Synthesis and Evaluation of pH-Sensitive Multifunctional Lipids for Efficient Delivery of CRISPR/Cas9 in Gene Editing.
Da Sun, Zhanhu Sun, Hongfa Jiang, Amita M Vaidya, Rui Xin, Nadia R Ayat, Andrew L Schilb, Peter L Qiao, Zheng Han, Amirreza Naderi,[...]. Bioconjug Chem 2019
14
28

Systemic Delivery of Tumor-Targeting siRNA Nanoparticles against an Oncogenic LncRNA Facilitates Effective Triple-Negative Breast Cancer Therapy.
Amita M Vaidya, Zhanhu Sun, Nadia Ayat, Andrew Schilb, Xujie Liu, Hongfa Jiang, Da Sun, Josef Scheidt, Victoria Qian, Siyuan He,[...]. Bioconjug Chem 2019
61
28

Safety and efficacy of gene transfer for Leber's congenital amaurosis.
Albert M Maguire, Francesca Simonelli, Eric A Pierce, Edward N Pugh, Federico Mingozzi, Jeannette Bennicelli, Sandro Banfi, Kathleen A Marshall, Francesco Testa, Enrico M Surace,[...]. N Engl J Med 2008
28

Three-year follow-up after unilateral subretinal delivery of adeno-associated virus in patients with Leber congenital Amaurosis type 2.
Francesco Testa, Albert M Maguire, Settimio Rossi, Eric A Pierce, Paolo Melillo, Kathleen Marshall, Sandro Banfi, Enrico M Surace, Junwei Sun, Carmela Acerra,[...]. Ophthalmology 2013
220
28

Two-Year Results After AAV2-Mediated Gene Therapy for Choroideremia: The Alberta Experience.
Ioannis S Dimopoulos, Stephanie C Hoang, Alina Radziwon, Natalia M Binczyk, Miguel C Seabra, Robert E MacLaren, Rizwan Somani, Matthew T S Tennant, Ian M MacDonald. Am J Ophthalmol 2018
75
28

In vivo-directed evolution of a new adeno-associated virus for therapeutic outer retinal gene delivery from the vitreous.
Deniz Dalkara, Leah C Byrne, Ryan R Klimczak, Meike Visel, Lu Yin, William H Merigan, John G Flannery, David V Schaffer. Sci Transl Med 2013
377
28

Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial.
Stephen Russell, Jean Bennett, Jennifer A Wellman, Daniel C Chung, Zi-Fan Yu, Amy Tillman, Janet Wittes, Julie Pappas, Okan Elci, Sarah McCague,[...]. Lancet 2017
617
28

Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR.
Jasmina Cehajic-Kapetanovic, Kanmin Xue, Cristina Martinez-Fernandez de la Camara, Anika Nanda, Alexandra Davies, Laura J Wood, Anna Paola Salvetti, M Dominik Fischer, James W Aylward, Alun R Barnard,[...]. Nat Med 2020
80
28

Correction of the disease phenotype in the mouse model of Stargardt disease by lentiviral gene therapy.
J Kong, S-R Kim, K Binley, I Pata, K Doi, J Mannik, J Zernant-Rajang, O Kan, S Iqball, S Naylor,[...]. Gene Ther 2008
144
28

Effective delivery of large genes to the retina by dual AAV vectors.
Ivana Trapani, Pasqualina Colella, Andrea Sommella, Carolina Iodice, Giulia Cesi, Sonia de Simone, Elena Marrocco, Settimio Rossi, Massimo Giunti, Arpad Palfi,[...]. EMBO Mol Med 2014
131
28

Effect of an intravitreal antisense oligonucleotide on vision in Leber congenital amaurosis due to a photoreceptor cilium defect.
Artur V Cideciyan, Samuel G Jacobson, Arlene V Drack, Allen C Ho, Jason Charng, Alexandra V Garafalo, Alejandro J Roman, Alexander Sumaroka, Ian C Han, Maria D Hochstedler,[...]. Nat Med 2019
107
28

The entry of nanoparticles into solid tumours.
Shrey Sindhwani, Abdullah Muhammad Syed, Jessica Ngai, Benjamin R Kingston, Laura Maiorino, Jeremy Rothschild, Presley MacMillan, Yuwei Zhang, Netra Unni Rajesh, Tran Hoang,[...]. Nat Mater 2020
349
21

FDA-Approved Oligonucleotide Therapies in 2017.
Cy A Stein, Daniela Castanotto. Mol Ther 2017
349
21

Gene therapy clinical trials worldwide to 2017: An update.
Samantha L Ginn, Anais K Amaya, Ian E Alexander, Michael Edelstein, Mohammad R Abedi. J Gene Med 2018
323
21


Image-based analysis of lipid nanoparticle-mediated siRNA delivery, intracellular trafficking and endosomal escape.
Jerome Gilleron, William Querbes, Anja Zeigerer, Anna Borodovsky, Giovanni Marsico, Undine Schubert, Kevin Manygoats, Sarah Seifert, Cordula Andree, Martin Stöter,[...]. Nat Biotechnol 2013
630
21

Choroideremia Gene Therapy Phase 2 Clinical Trial: 24-Month Results.
Byron L Lam, Janet L Davis, Ninel Z Gregori, Robert E MacLaren, Aniz Girach, Jennifer D Verriotto, Belen Rodriguez, Potyra R Rosa, Xiaojun Zhang, William J Feuer. Am J Ophthalmol 2019
68
21

Efficacy, Safety, and Durability of Voretigene Neparvovec-rzyl in RPE65 Mutation-Associated Inherited Retinal Dystrophy: Results of Phase 1 and 3 Trials.
Albert M Maguire, Stephen Russell, Jennifer A Wellman, Daniel C Chung, Zi-Fan Yu, Amy Tillman, Janet Wittes, Julie Pappas, Okan Elci, Kathleen A Marshall,[...]. Ophthalmology 2019
106
21

DNA nanoparticles are safe and nontoxic in non-human primate eyes.
Ryan A Kelley, Shannon M Conley, Rasha Makkia, Jamie N Watson, Zongchao Han, Mark J Cooper, Muna I Naash. Int J Nanomedicine 2018
15
21

Beneficial effects on vision in patients undergoing retinal gene therapy for choroideremia.
Kanmin Xue, Jasleen K Jolly, Alun R Barnard, Anna Rudenko, Anna P Salvetti, Maria I Patrício, Thomas L Edwards, Markus Groppe, Harry O Orlans, Tanya Tolmachova,[...]. Nat Med 2018
79
21

Treatment of retinitis pigmentosa due to MERTK mutations by ocular subretinal injection of adeno-associated virus gene vector: results of a phase I trial.
Nicola G Ghazi, Emad B Abboud, Sawsan R Nowilaty, Hisham Alkuraya, Abdulrahman Alhommadi, Huimin Cai, Rui Hou, Wen-Tao Deng, Sanford L Boye, Abdulrahman Almaghamsi,[...]. Hum Genet 2016
130
21

Safety and Vision Outcomes of Subretinal Gene Therapy Targeting Cone Photoreceptors in Achromatopsia: A Nonrandomized Controlled Trial.
M Dominik Fischer, Stylianos Michalakis, Barbara Wilhelm, Ditta Zobor, Regine Muehlfriedel, Susanne Kohl, Nicole Weisschuh, G Alex Ochakovski, Reinhild Klein, Christian Schoen,[...]. JAMA Ophthalmol 2020
39
21


Adeno-Associated Viral Gene Therapy for Inherited Retinal Disease.
Tuyen Ong, Mark E Pennesi, David G Birch, Byron L Lam, Stephen H Tsang. Pharm Res 2019
19
21

Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery.
Catherine Cukras, Henry E Wiley, Brett G Jeffrey, H Nida Sen, Amy Turriff, Yong Zeng, Camasamudram Vijayasarathy, Dario Marangoni, Lucia Ziccardi, Sten Kjellstrom,[...]. Mol Ther 2018
88
21

Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial.
Albert M Maguire, Katherine A High, Alberto Auricchio, J Fraser Wright, Eric A Pierce, Francesco Testa, Federico Mingozzi, Jeannette L Bennicelli, Gui-shuang Ying, Settimio Rossi,[...]. Lancet 2009
581
21

Ocular immune privilege.
Ru Zhou, Rachel R Caspi. F1000 Biol Rep 2010
102
21

Self-Assembly of a Multifunctional Lipid With Core-Shell Dendrimer DNA Nanoparticles Enhanced Efficient Gene Delivery at Low Charge Ratios into RPE Cells.
Da Sun, Hiroshi Maeno, Maneesh Gujrati, Rebecca Schur, Akiko Maeda, Tadao Maeda, Krzysztof Palczewski, Zheng-Rong Lu. Macromol Biosci 2015
19
21

Mutation Spectrum of the ABCA4 Gene in 335 Stargardt Disease Patients From a Multicenter German Cohort-Impact of Selected Deep Intronic Variants and Common SNPs.
Heidi L Schulz, Felix Grassmann, Ulrich Kellner, Georg Spital, Klaus Rüther, Herbert Jägle, Karsten Hufendiek, Philipp Rating, Cord Huchzermeyer, Maria J Baier,[...]. Invest Ophthalmol Vis Sci 2017
70
21

Effect of genome size on AAV vector packaging.
Zhijian Wu, Hongyan Yang, Peter Colosi. Mol Ther 2010
427
21

Persistence of non-viral vector mediated RPE65 expression: case for viability as a gene transfer therapy for RPE-based diseases.
Adarsha Koirala, Shannon M Conley, Rasha Makkia, Zhao Liu, Mark J Cooper, Janet R Sparrow, Muna I Naash. J Control Release 2013
24
21

Mutation-independent rhodopsin gene therapy by knockdown and replacement with a single AAV vector.
Artur V Cideciyan, Raghavi Sudharsan, Valérie L Dufour, Michael T Massengill, Simone Iwabe, Malgorzata Swider, Brianna Lisi, Alexander Sumaroka, Luis Felipe Marinho, Tatyana Appelbaum,[...]. Proc Natl Acad Sci U S A 2018
68
21

Treatment of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial.
William W Hauswirth, Tomas S Aleman, Shalesh Kaushal, Artur V Cideciyan, Sharon B Schwartz, Lili Wang, Thomas J Conlon, Sanford L Boye, Terence R Flotte, Barry J Byrne,[...]. Hum Gene Ther 2008
705
21

ABCA4 is an N-retinylidene-phosphatidylethanolamine and phosphatidylethanolamine importer.
Faraz Quazi, Stepan Lenevich, Robert S Molday. Nat Commun 2012
144
21

Correlating the Expression and Functional Activity of ABCA4 Disease Variants With the Phenotype of Patients With Stargardt Disease.
Fabian Garces, Kailun Jiang, Laurie L Molday, Heidi Stöhr, Bernhard H Weber, Christopher J Lyons, David Maberley, Robert S Molday. Invest Ophthalmol Vis Sci 2018
25
21

Identification and Rescue of Splice Defects Caused by Two Neighboring Deep-Intronic ABCA4 Mutations Underlying Stargardt Disease.
Silvia Albert, Alejandro Garanto, Riccardo Sangermano, Mubeen Khan, Nathalie M Bax, Carel B Hoyng, Jana Zernant, Winston Lee, Rando Allikmets, Rob W J Collin,[...]. Am J Hum Genet 2018
52
21

ABCA4 midigenes reveal the full splice spectrum of all reported noncanonical splice site variants in Stargardt disease.
Riccardo Sangermano, Mubeen Khan, Stéphanie S Cornelis, Valerie Richelle, Silvia Albert, Alejandro Garanto, Duaa Elmelik, Raheel Qamar, Dorien Lugtenberg, L Ingeborgh van den Born,[...]. Genome Res 2018
66
21

Development of a gene-editing approach to restore vision loss in Leber congenital amaurosis type 10.
Morgan L Maeder, Michael Stefanidakis, Christopher J Wilson, Reshica Baral, Luis Alberto Barrera, George S Bounoutas, David Bumcrot, Hoson Chao, Dawn M Ciulla, Jennifer A DaSilva,[...]. Nat Med 2019
214
21


Detailed Phenotyping and Therapeutic Strategies for Intronic ABCA4 Variants in Stargardt Disease.
Mubeen Khan, Gavin Arno, Ana Fakin, David A Parfitt, Patty P A Dhooge, Silvia Albert, Nathalie M Bax, Lonneke Duijkers, Michael Niblock, Kwan L Hau,[...]. Mol Ther Nucleic Acids 2020
12
25

Transduction of photoreceptors with equine infectious anemia virus lentiviral vectors: safety and biodistribution of StarGen for Stargardt disease.
Katie Binley, Peter Widdowson, Julie Loader, Michelle Kelleher, Sharifah Iqball, Georgina Ferrige, Jackie de Belin, Marie Carlucci, Diana Angell-Manning, Felicity Hurst,[...]. Invest Ophthalmol Vis Sci 2013
73
21

ABCA4-associated disease as a model for missing heritability in autosomal recessive disorders: novel noncoding splice, cis-regulatory, structural, and recurrent hypomorphic variants.
Miriam Bauwens, Alejandro Garanto, Riccardo Sangermano, Sarah Naessens, Nicole Weisschuh, Julie De Zaeytijd, Mubeen Khan, Françoise Sadler, Irina Balikova, Caroline Van Cauwenbergh,[...]. Genet Med 2019
45
21

Non-exomic and synonymous variants in ABCA4 are an important cause of Stargardt disease.
Terry A Braun, Robert F Mullins, Alex H Wagner, Jeaneen L Andorf, Rebecca M Johnston, Benjamin B Bakall, Adam P Deluca, Gerald A Fishman, Byron L Lam, Richard G Weleber,[...]. Hum Mol Genet 2013
106
21


Co-cited is the co-citation frequency, indicating how many articles cite the article together with the query article. Similarity is the co-citation as percentage of the times cited of the query article or the article in the search results, whichever is the lowest. These numbers are calculated for the last 100 citations when articles are cited more than 100 times.