Katelin M Allan, Nigel Farrow, Martin Donnelley, Adam Jaffe, Shafagh A Waters. Front Pharmacol 2021
Times Cited: 4
Times Cited: 4
Times Cited
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Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis.
Eric W F W Alton, Jeffery M Beekman, A Christopher Boyd, June Brand, Marianne S Carlon, Mary M Connolly, Mario Chan, Sinead Conlon, Heather E Davidson, Jane C Davies,[...]. Thorax 2017
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Ashley L Cooney, Paul B McCray, Patrick L Sinn. Genes (Basel) 2018
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Comparative proteomics of respiratory exosomes in cystic fibrosis, primary ciliary dyskinesia and asthma.
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Engineered transfer RNAs for suppression of premature termination codons.
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Correlating Cystic Fibrosis Transmembrane Conductance Regulator Function with Clinical Features to Inform Precision Treatment of Cystic Fibrosis.
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Ataluren for the treatment of nonsense-mutation cystic fibrosis: a randomised, double-blind, placebo-controlled phase 3 trial.
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Aerosolizable Lipid Nanoparticles for Pulmonary Delivery of mRNA through Design of Experiments.
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Modulators of CFTR. Updates on clinical development and future directions.
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Correction to: In vitro prediction of stop-codon suppression by intravenous gentamicin in patients with cystic fibrosis: a pilot study.
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Cell Therapy for Cystic Fibrosis Lung Disease: Regenerative Basal Cell Amplification.
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Correction of a Cystic Fibrosis Splicing Mutation by Antisense Oligonucleotides.
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Therapeutic promise of engineered nonsense suppressor tRNAs.
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Nonsense-mediated RNA Decay Pathway Inhibition Restores Expression and Function of W1282X CFTR.
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New approaches to genetic therapies for cystic fibrosis.
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Antisense oligonucleotide-mediated correction of CFTR splicing improves chloride secretion in cystic fibrosis patient-derived bronchial epithelial cells.
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Delivering on the promise of gene editing for cystic fibrosis.
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Mesenchymal Stem Cell exosome delivered Zinc Finger Protein activation of cystic fibrosis transmembrane conductance regulator.
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Challenges Facing Airway Epithelial Cell-Based Therapy for Cystic Fibrosis.
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Antisense oligonucleotide eluforsen improves CFTR function in F508del cystic fibrosis.
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Functional repair of CFTR by CRISPR/Cas9 in intestinal stem cell organoids of cystic fibrosis patients.
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mRNA as a versatile tool for exogenous protein expression.
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Aminoglycoside antibiotics restore CFTR function by overcoming premature stop mutations.
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Managing cystic fibrosis: strategies that increase life expectancy and improve quality of life.
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Splicing regulation as a potential genetic modifier.
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Lipid Nanoparticle-Delivered Chemically Modified mRNA Restores Chloride Secretion in Cystic Fibrosis.
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Efficient Gene Editing at Major CFTR Mutation Loci.
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Evaluation of eluforsen, a novel RNA oligonucleotide for restoration of CFTR function in in vitro and murine models of p.Phe508del cystic fibrosis.
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Treating Cystic Fibrosis with mRNA and CRISPR.
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Antisense oligonucleotide eluforsen is safe and improves respiratory symptoms in F508DEL cystic fibrosis.
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Co-cited is the co-citation frequency, indicating how many articles cite the article together with the query article. Similarity is the co-citation as percentage of the times cited of the query article or the article in the search results, whichever is the lowest. These numbers are calculated for the last 100 citations when articles are cited more than 100 times.