Eman A Taha, Joseph Lee, Akitsu Hotta. J Control Release 2022
Times Cited: 13
Times Cited: 13
Times Cited
Times Co-cited
Similarity
A programmable dual-RNA-guided DNA endonuclease in adaptive bacterial immunity.
Martin Jinek, Krzysztof Chylinski, Ines Fonfara, Michael Hauer, Jennifer A Doudna, Emmanuelle Charpentier. Science 2012
Martin Jinek, Krzysztof Chylinski, Ines Fonfara, Michael Hauer, Jennifer A Doudna, Emmanuelle Charpentier. Science 2012
53
Search-and-replace genome editing without double-strand breaks or donor DNA.
Andrew V Anzalone, Peyton B Randolph, Jessie R Davis, Alexander A Sousa, Luke W Koblan, Jonathan M Levy, Peter J Chen, Christopher Wilson, Gregory A Newby, Aditya Raguram,[...]. Nature 2019
Andrew V Anzalone, Peyton B Randolph, Jessie R Davis, Alexander A Sousa, Luke W Koblan, Jonathan M Levy, Peter J Chen, Christopher Wilson, Gregory A Newby, Aditya Raguram,[...]. Nature 2019
46
RNA-guided human genome engineering via Cas9.
Prashant Mali, Luhan Yang, Kevin M Esvelt, John Aach, Marc Guell, James E DiCarlo, Julie E Norville, George M Church. Science 2013
Prashant Mali, Luhan Yang, Kevin M Esvelt, John Aach, Marc Guell, James E DiCarlo, Julie E Norville, George M Church. Science 2013
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Multiplex genome engineering using CRISPR/Cas systems.
Le Cong, F Ann Ran, David Cox, Shuailiang Lin, Robert Barretto, Naomi Habib, Patrick D Hsu, Xuebing Wu, Wenyan Jiang, Luciano A Marraffini,[...]. Science 2013
Le Cong, F Ann Ran, David Cox, Shuailiang Lin, Robert Barretto, Naomi Habib, Patrick D Hsu, Xuebing Wu, Wenyan Jiang, Luciano A Marraffini,[...]. Science 2013
38
CRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis.
Julian D Gillmore, Ed Gane, Jorg Taubel, Justin Kao, Marianna Fontana, Michael L Maitland, Jessica Seitzer, Daniel O'Connell, Kathryn R Walsh, Kristy Wood,[...]. N Engl J Med 2021
Julian D Gillmore, Ed Gane, Jorg Taubel, Justin Kao, Marianna Fontana, Michael L Maitland, Jessica Seitzer, Daniel O'Connell, Kathryn R Walsh, Kristy Wood,[...]. N Engl J Med 2021
38
A Single Administration of CRISPR/Cas9 Lipid Nanoparticles Achieves Robust and Persistent In Vivo Genome Editing.
Jonathan D Finn, Amy Rhoden Smith, Mihir C Patel, Lucinda Shaw, Madeleine R Youniss, Jane van Heteren, Tanner Dirstine, Corey Ciullo, Reynald Lescarbeau, Jessica Seitzer,[...]. Cell Rep 2018
Jonathan D Finn, Amy Rhoden Smith, Mihir C Patel, Lucinda Shaw, Madeleine R Youniss, Jane van Heteren, Tanner Dirstine, Corey Ciullo, Reynald Lescarbeau, Jessica Seitzer,[...]. Cell Rep 2018
38
Programmable editing of a target base in genomic DNA without double-stranded DNA cleavage.
Alexis C Komor, Yongjoo B Kim, Michael S Packer, John A Zuris, David R Liu. Nature 2016
Alexis C Komor, Yongjoo B Kim, Michael S Packer, John A Zuris, David R Liu. Nature 2016
38
Rational designs of in vivo CRISPR-Cas delivery systems.
Cong-Fei Xu, Guo-Jun Chen, Ying-Li Luo, Yue Zhang, Gui Zhao, Zi-Dong Lu, Anna Czarna, Zhen Gu, Jun Wang. Adv Drug Deliv Rev 2021
Cong-Fei Xu, Guo-Jun Chen, Ying-Li Luo, Yue Zhang, Gui Zhao, Zi-Dong Lu, Anna Czarna, Zhen Gu, Jun Wang. Adv Drug Deliv Rev 2021
38
Non-Viral CRISPR/Cas Gene Editing In Vitro and In Vivo Enabled by Synthetic Nanoparticle Co-Delivery of Cas9 mRNA and sgRNA.
Jason B Miller, Shuyuan Zhang, Petra Kos, Hu Xiong, Kejin Zhou, Sofya S Perelman, Hao Zhu, Daniel J Siegwart. Angew Chem Int Ed Engl 2017
Jason B Miller, Shuyuan Zhang, Petra Kos, Hu Xiong, Kejin Zhou, Sofya S Perelman, Hao Zhu, Daniel J Siegwart. Angew Chem Int Ed Engl 2017
38
In vivo genome editing using Staphylococcus aureus Cas9.
F Ann Ran, Le Cong, Winston X Yan, David A Scott, Jonathan S Gootenberg, Andrea J Kriz, Bernd Zetsche, Ophir Shalem, Xuebing Wu, Kira S Makarova,[...]. Nature 2015
F Ann Ran, Le Cong, Winston X Yan, David A Scott, Jonathan S Gootenberg, Andrea J Kriz, Bernd Zetsche, Ophir Shalem, Xuebing Wu, Kira S Makarova,[...]. Nature 2015
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CRISPR provides acquired resistance against viruses in prokaryotes.
Rodolphe Barrangou, Christophe Fremaux, Hélène Deveau, Melissa Richards, Patrick Boyaval, Sylvain Moineau, Dennis A Romero, Philippe Horvath. Science 2007
Rodolphe Barrangou, Christophe Fremaux, Hélène Deveau, Melissa Richards, Patrick Boyaval, Sylvain Moineau, Dennis A Romero, Philippe Horvath. Science 2007
30
Delivering CRISPR: a review of the challenges and approaches.
Christopher A Lino, Jason C Harper, James P Carney, Jerilyn A Timlin. Drug Deliv 2018
Christopher A Lino, Jason C Harper, James P Carney, Jerilyn A Timlin. Drug Deliv 2018
30
Delivery strategies of the CRISPR-Cas9 gene-editing system for therapeutic applications.
Chang Liu, Li Zhang, Hao Liu, Kun Cheng. J Control Release 2017
Chang Liu, Li Zhang, Hao Liu, Kun Cheng. J Control Release 2017
30
Nanoparticle delivery of Cas9 ribonucleoprotein and donor DNA in vivo induces homology-directed DNA repair.
Kunwoo Lee, Michael Conboy, Hyo Min Park, Fuguo Jiang, Hyun Jin Kim, Mark A Dewitt, Vanessa A Mackley, Kevin Chang, Anirudh Rao, Colin Skinner,[...]. Nat Biomed Eng 2017
Kunwoo Lee, Michael Conboy, Hyo Min Park, Fuguo Jiang, Hyun Jin Kim, Mark A Dewitt, Vanessa A Mackley, Kevin Chang, Anirudh Rao, Colin Skinner,[...]. Nat Biomed Eng 2017
30
Fast and Efficient CRISPR/Cas9 Genome Editing In Vivo Enabled by Bioreducible Lipid and Messenger RNA Nanoparticles.
Ji Liu, Jin Chang, Ying Jiang, Xiandi Meng, Tianmeng Sun, Lanqun Mao, Qiaobing Xu, Ming Wang. Adv Mater 2019
Ji Liu, Jin Chang, Ying Jiang, Xiandi Meng, Tianmeng Sun, Lanqun Mao, Qiaobing Xu, Ming Wang. Adv Mater 2019
30
A biodegradable nanocapsule delivers a Cas9 ribonucleoprotein complex for in vivo genome editing.
Guojun Chen, Amr A Abdeen, Yuyuan Wang, Pawan K Shahi, Samantha Robertson, Ruosen Xie, Masatoshi Suzuki, Bikash R Pattnaik, Krishanu Saha, Shaoqin Gong. Nat Nanotechnol 2019
Guojun Chen, Amr A Abdeen, Yuyuan Wang, Pawan K Shahi, Samantha Robertson, Ruosen Xie, Masatoshi Suzuki, Bikash R Pattnaik, Krishanu Saha, Shaoqin Gong. Nat Nanotechnol 2019
30
Cas9 protein delivery non-integrating lentiviral vectors for gene correction in sickle cell disease.
Naoya Uchida, Claire M Drysdale, Tina Nassehi, Jackson Gamer, Morgan Yapundich, Julia DiNicola, Yoshitaka Shibata, Malikiya Hinds, Bjorg Gudmundsdottir, Juan J Haro-Mora,[...]. Mol Ther Methods Clin Dev 2021
Naoya Uchida, Claire M Drysdale, Tina Nassehi, Jackson Gamer, Morgan Yapundich, Julia DiNicola, Yoshitaka Shibata, Malikiya Hinds, Bjorg Gudmundsdottir, Juan J Haro-Mora,[...]. Mol Ther Methods Clin Dev 2021
23
Efficient delivery of genome-editing proteins using bioreducible lipid nanoparticles.
Ming Wang, John A Zuris, Fantao Meng, Holly Rees, Shuo Sun, Pu Deng, Yong Han, Xue Gao, Dimitra Pouli, Qi Wu,[...]. Proc Natl Acad Sci U S A 2016
Ming Wang, John A Zuris, Fantao Meng, Holly Rees, Shuo Sun, Pu Deng, Yong Han, Xue Gao, Dimitra Pouli, Qi Wu,[...]. Proc Natl Acad Sci U S A 2016
23
Delivery Aspects of CRISPR/Cas for in Vivo Genome Editing.
Danny Wilbie, Johanna Walther, Enrico Mastrobattista. Acc Chem Res 2019
Danny Wilbie, Johanna Walther, Enrico Mastrobattista. Acc Chem Res 2019
23
Engineering adeno-associated virus vectors for gene therapy.
Chengwen Li, R Jude Samulski. Nat Rev Genet 2020
Chengwen Li, R Jude Samulski. Nat Rev Genet 2020
23
DNA targeting specificity of RNA-guided Cas9 nucleases.
Patrick D Hsu, David A Scott, Joshua A Weinstein, F Ann Ran, Silvana Konermann, Vineeta Agarwala, Yinqing Li, Eli J Fine, Xuebing Wu, Ophir Shalem,[...]. Nat Biotechnol 2013
Patrick D Hsu, David A Scott, Joshua A Weinstein, F Ann Ran, Silvana Konermann, Vineeta Agarwala, Yinqing Li, Eli J Fine, Xuebing Wu, Ophir Shalem,[...]. Nat Biotechnol 2013
23
High levels of AAV vector integration into CRISPR-induced DNA breaks.
Killian S Hanlon, Benjamin P Kleinstiver, Sara P Garcia, Mikołaj P Zaborowski, Adrienn Volak, Stefan E Spirig, Alissa Muller, Alexander A Sousa, Shengdar Q Tsai, Niclas E Bengtsson,[...]. Nat Commun 2019
Killian S Hanlon, Benjamin P Kleinstiver, Sara P Garcia, Mikołaj P Zaborowski, Adrienn Volak, Stefan E Spirig, Alissa Muller, Alexander A Sousa, Shengdar Q Tsai, Niclas E Bengtsson,[...]. Nat Commun 2019
23
The Onpattro story and the clinical translation of nanomedicines containing nucleic acid-based drugs.
Akin Akinc, Martin A Maier, Muthiah Manoharan, Kevin Fitzgerald, Muthusamy Jayaraman, Scott Barros, Steven Ansell, Xinyao Du, Michael J Hope, Thomas D Madden,[...]. Nat Nanotechnol 2019
Akin Akinc, Martin A Maier, Muthiah Manoharan, Kevin Fitzgerald, Muthusamy Jayaraman, Scott Barros, Steven Ansell, Xinyao Du, Michael J Hope, Thomas D Madden,[...]. Nat Nanotechnol 2019
23
Lipid nanoparticles loaded with ribonucleoprotein-oligonucleotide complexes synthesized using a microfluidic device exhibit robust genome editing and hepatitis B virus inhibition.
Yuichi Suzuki, Haruno Onuma, Risa Sato, Yusuke Sato, Akari Hashiba, Masatoshi Maeki, Manabu Tokeshi, Mohammad Enamul Hoque Kayesh, Michinori Kohara, Kyoko Tsukiyama-Kohara,[...]. J Control Release 2021
Yuichi Suzuki, Haruno Onuma, Risa Sato, Yusuke Sato, Akari Hashiba, Masatoshi Maeki, Manabu Tokeshi, Mohammad Enamul Hoque Kayesh, Michinori Kohara, Kyoko Tsukiyama-Kohara,[...]. J Control Release 2021
23
High-fidelity CRISPR-Cas9 nucleases with no detectable genome-wide off-target effects.
Benjamin P Kleinstiver, Vikram Pattanayak, Michelle S Prew, Shengdar Q Tsai, Nhu T Nguyen, Zongli Zheng, J Keith Joung. Nature 2016
Benjamin P Kleinstiver, Vikram Pattanayak, Michelle S Prew, Shengdar Q Tsai, Nhu T Nguyen, Zongli Zheng, J Keith Joung. Nature 2016
23
Targeted nucleotide editing using hybrid prokaryotic and vertebrate adaptive immune systems.
Keiji Nishida, Takayuki Arazoe, Nozomu Yachie, Satomi Banno, Mika Kakimoto, Mayura Tabata, Masao Mochizuki, Aya Miyabe, Michihiro Araki, Kiyotaka Y Hara,[...]. Science 2016
Keiji Nishida, Takayuki Arazoe, Nozomu Yachie, Satomi Banno, Mika Kakimoto, Mayura Tabata, Masao Mochizuki, Aya Miyabe, Michihiro Araki, Kiyotaka Y Hara,[...]. Science 2016
23
Development of an intein-mediated split-Cas9 system for gene therapy.
Dong-Jiunn Jeffery Truong, Karin Kühner, Ralf Kühn, Stanislas Werfel, Stefan Engelhardt, Wolfgang Wurst, Oskar Ortiz. Nucleic Acids Res 2015
Dong-Jiunn Jeffery Truong, Karin Kühner, Ralf Kühn, Stanislas Werfel, Stefan Engelhardt, Wolfgang Wurst, Oskar Ortiz. Nucleic Acids Res 2015
23
High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells.
Yanfang Fu, Jennifer A Foden, Cyd Khayter, Morgan L Maeder, Deepak Reyon, J Keith Joung, Jeffry D Sander. Nat Biotechnol 2013
Yanfang Fu, Jennifer A Foden, Cyd Khayter, Morgan L Maeder, Deepak Reyon, J Keith Joung, Jeffry D Sander. Nat Biotechnol 2013
23
Thermo-triggered Release of CRISPR-Cas9 System by Lipid-Encapsulated Gold Nanoparticles for Tumor Therapy.
Peng Wang, Lingmin Zhang, Wenfu Zheng, Liman Cong, Zhaorong Guo, Yangzhouyun Xie, Le Wang, Rongbing Tang, Qiang Feng, Yoh Hamada,[...]. Angew Chem Int Ed Engl 2018
Peng Wang, Lingmin Zhang, Wenfu Zheng, Liman Cong, Zhaorong Guo, Yangzhouyun Xie, Le Wang, Rongbing Tang, Qiang Feng, Yoh Hamada,[...]. Angew Chem Int Ed Engl 2018
23
Systemic nanoparticle delivery of CRISPR-Cas9 ribonucleoproteins for effective tissue specific genome editing.
Tuo Wei, Qiang Cheng, Yi-Li Min, Eric N Olson, Daniel J Siegwart. Nat Commun 2020
Tuo Wei, Qiang Cheng, Yi-Li Min, Eric N Olson, Daniel J Siegwart. Nat Commun 2020
23
Programmable base editing of A•T to G•C in genomic DNA without DNA cleavage.
Nicole M Gaudelli, Alexis C Komor, Holly A Rees, Michael S Packer, Ahmed H Badran, David I Bryson, David R Liu. Nature 2017
Nicole M Gaudelli, Alexis C Komor, Holly A Rees, Michael S Packer, Ahmed H Badran, David I Bryson, David R Liu. Nature 2017
23
Prevalence of Pre-existing Antibodies to CRISPR-Associated Nuclease Cas9 in the USA Population.
Vijaya L Simhadri, Joseph McGill, Shane McMahon, Junxia Wang, Haiyan Jiang, Zuben E Sauna. Mol Ther Methods Clin Dev 2018
Vijaya L Simhadri, Joseph McGill, Shane McMahon, Junxia Wang, Haiyan Jiang, Zuben E Sauna. Mol Ther Methods Clin Dev 2018
23
Engineering the Delivery System for CRISPR-Based Genome Editing.
Zachary Glass, Matthew Lee, Yamin Li, Qiaobing Xu. Trends Biotechnol 2018
Zachary Glass, Matthew Lee, Yamin Li, Qiaobing Xu. Trends Biotechnol 2018
23
Selective organ targeting (SORT) nanoparticles for tissue-specific mRNA delivery and CRISPR-Cas gene editing.
Qiang Cheng, Tuo Wei, Lukas Farbiak, Lindsay T Johnson, Sean A Dilliard, Daniel J Siegwart. Nat Nanotechnol 2020
Qiang Cheng, Tuo Wei, Lukas Farbiak, Lindsay T Johnson, Sean A Dilliard, Daniel J Siegwart. Nat Nanotechnol 2020
23
High-throughput in vivo screen of functional mRNA delivery identifies nanoparticles for endothelial cell gene editing.
Cory D Sago, Melissa P Lokugamage, Kalina Paunovska, Daryll A Vanover, Christopher M Monaco, Nirav N Shah, Marielena Gamboa Castro, Shannon E Anderson, Tobi G Rudoltz, Gwyneth N Lando,[...]. Proc Natl Acad Sci U S A 2018
Cory D Sago, Melissa P Lokugamage, Kalina Paunovska, Daryll A Vanover, Christopher M Monaco, Nirav N Shah, Marielena Gamboa Castro, Shannon E Anderson, Tobi G Rudoltz, Gwyneth N Lando,[...]. Proc Natl Acad Sci U S A 2018
23
Chromothripsis as an on-target consequence of CRISPR-Cas9 genome editing.
Mitchell L Leibowitz, Stamatis Papathanasiou, Phillip A Doerfler, Logan J Blaine, Lili Sun, Yu Yao, Cheng-Zhong Zhang, Mitchell J Weiss, David Pellman. Nat Genet 2021
Mitchell L Leibowitz, Stamatis Papathanasiou, Phillip A Doerfler, Logan J Blaine, Lili Sun, Yu Yao, Cheng-Zhong Zhang, Mitchell J Weiss, David Pellman. Nat Genet 2021
23
Targeted delivery of CRISPR-Cas9 and transgenes enables complex immune cell engineering.
Jennifer R Hamilton, Connor A Tsuchida, David N Nguyen, Brian R Shy, E Riley McGarrigle, Cindy R Sandoval Espinoza, Daniel Carr, Franziska Blaeschke, Alexander Marson, Jennifer A Doudna. Cell Rep 2021
Jennifer R Hamilton, Connor A Tsuchida, David N Nguyen, Brian R Shy, E Riley McGarrigle, Cindy R Sandoval Espinoza, Daniel Carr, Franziska Blaeschke, Alexander Marson, Jennifer A Doudna. Cell Rep 2021
23
Cationic lipid-mediated delivery of proteins enables efficient protein-based genome editing in vitro and in vivo.
John A Zuris, David B Thompson, Yilai Shu, John P Guilinger, Jeffrey L Bessen, Johnny H Hu, Morgan L Maeder, J Keith Joung, Zheng-Yi Chen, David R Liu. Nat Biotechnol 2015
John A Zuris, David B Thompson, Yilai Shu, John P Guilinger, Jeffrey L Bessen, Johnny H Hu, Morgan L Maeder, J Keith Joung, Zheng-Yi Chen, David R Liu. Nat Biotechnol 2015
23
Genome editing with CRISPR-Cas nucleases, base editors, transposases and prime editors.
Andrew V Anzalone, Luke W Koblan, David R Liu. Nat Biotechnol 2020
Andrew V Anzalone, Luke W Koblan, David R Liu. Nat Biotechnol 2020
23
CRISPR-Based Therapeutic Genome Editing: Strategies and In Vivo Delivery by AAV Vectors.
Dan Wang, Feng Zhang, Guangping Gao. Cell 2020
Dan Wang, Feng Zhang, Guangping Gao. Cell 2020
23
Identification of preexisting adaptive immunity to Cas9 proteins in humans.
Carsten T Charlesworth, Priyanka S Deshpande, Daniel P Dever, Joab Camarena, Viktor T Lemgart, M Kyle Cromer, Christopher A Vakulskas, Michael A Collingwood, Liyang Zhang, Nicole M Bode,[...]. Nat Med 2019
Carsten T Charlesworth, Priyanka S Deshpande, Daniel P Dever, Joab Camarena, Viktor T Lemgart, M Kyle Cromer, Christopher A Vakulskas, Michael A Collingwood, Liyang Zhang, Nicole M Bode,[...]. Nat Med 2019
23
Engineering Delivery Vehicles for Genome Editing.
Christopher E Nelson, Charles A Gersbach. Annu Rev Chem Biomol Eng 2016
Christopher E Nelson, Charles A Gersbach. Annu Rev Chem Biomol Eng 2016
23
Latest Developed Strategies to Minimize the Off-Target Effects in CRISPR-Cas-Mediated Genome Editing.
Muhammad Naeem, Saman Majeed, Mubasher Zahir Hoque, Irshad Ahmad. Cells 2020
Muhammad Naeem, Saman Majeed, Mubasher Zahir Hoque, Irshad Ahmad. Cells 2020
23
Virus-like nanoparticle as a co-delivery system to enhance efficacy of CRISPR/Cas9-based cancer immunotherapy.
Qi Liu, Chun Wang, Yadan Zheng, Yu Zhao, Ying Wang, Jialei Hao, Xinzhi Zhao, Kaikai Yi, Linqi Shi, Chunsheng Kang,[...]. Biomaterials 2020
Qi Liu, Chun Wang, Yadan Zheng, Yu Zhao, Ying Wang, Jialei Hao, Xinzhi Zhao, Kaikai Yi, Linqi Shi, Chunsheng Kang,[...]. Biomaterials 2020
23
Endosomal Escape and Delivery of CRISPR/Cas9 Genome Editing Machinery Enabled by Nanoscale Zeolitic Imidazolate Framework.
Shahad K Alsaiari, Sachin Patil, Mram Alyami, Kholod O Alamoudi, Fajr A Aleisa, Jasmeen S Merzaban, Mo Li, Niveen M Khashab. J Am Chem Soc 2018
Shahad K Alsaiari, Sachin Patil, Mram Alyami, Kholod O Alamoudi, Fajr A Aleisa, Jasmeen S Merzaban, Mo Li, Niveen M Khashab. J Am Chem Soc 2018
23
Co-delivery of Sorafenib and CRISPR/Cas9 Based on Targeted Core-Shell Hollow Mesoporous Organosilica Nanoparticles for Synergistic HCC Therapy.
Bing-Chen Zhang, Bang-Yue Luo, Jun-Jie Zou, Peng-Yu Wu, Jia-Li Jiang, Jing-Qing Le, Rui-Rui Zhao, Lu Chen, Jing-Wei Shao. ACS Appl Mater Interfaces 2020
Bing-Chen Zhang, Bang-Yue Luo, Jun-Jie Zou, Peng-Yu Wu, Jia-Li Jiang, Jing-Qing Le, Rui-Rui Zhao, Lu Chen, Jing-Wei Shao. ACS Appl Mater Interfaces 2020
23
CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cells.
Daniel P Dever, Rasmus O Bak, Andreas Reinisch, Joab Camarena, Gabriel Washington, Carmencita E Nicolas, Mara Pavel-Dinu, Nivi Saxena, Alec B Wilkens, Sruthi Mantri,[...]. Nature 2016
Daniel P Dever, Rasmus O Bak, Andreas Reinisch, Joab Camarena, Gabriel Washington, Carmencita E Nicolas, Mara Pavel-Dinu, Nivi Saxena, Alec B Wilkens, Sruthi Mantri,[...]. Nature 2016
15
Genome engineering using the CRISPR-Cas9 system.
F Ann Ran, Patrick D Hsu, Jason Wright, Vineeta Agarwala, David A Scott, Feng Zhang. Nat Protoc 2013
F Ann Ran, Patrick D Hsu, Jason Wright, Vineeta Agarwala, David A Scott, Feng Zhang. Nat Protoc 2013
15
Severe Toxicity in Nonhuman Primates and Piglets Following High-Dose Intravenous Administration of an Adeno-Associated Virus Vector Expressing Human SMN.
Christian Hinderer, Nathan Katz, Elizabeth L Buza, Cecilia Dyer, Tamara Goode, Peter Bell, Laura K Richman, James M Wilson. Hum Gene Ther 2018
Christian Hinderer, Nathan Katz, Elizabeth L Buza, Cecilia Dyer, Tamara Goode, Peter Bell, Laura K Richman, James M Wilson. Hum Gene Ther 2018
15
Co-cited is the co-citation frequency, indicating how many articles cite the article together with the query article. Similarity is the co-citation as percentage of the times cited of the query article or the article in the search results, whichever is the lowest. These numbers are calculated for the last 100 citations when articles are cited more than 100 times.