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Times Cited: 457
Chengwen Li, R Jude Samulski. Nat Rev Genet 2020
Times Cited: 247
Times Cited: 247
List of shared articles
Times cited
dCas9-VPR-mediated transcriptional activation of functionally equivalent genes for gene therapy.
Lisa M Riedmayr, Klara S Hinrichsmeyer, Nina Karguth, Sybille Böhm, Victoria Splith, Stylianos Michalakis, Elvir Becirovic. Nat Protoc 2022
Lisa M Riedmayr, Klara S Hinrichsmeyer, Nina Karguth, Sybille Böhm, Victoria Splith, Stylianos Michalakis, Elvir Becirovic. Nat Protoc 2022
AAV-mediated delivery of an anti-BACE1 VHH alleviates pathology in an Alzheimer's disease model.
Marika Marino, Lujia Zhou, Melvin Y Rincon, Zsuzsanna Callaerts-Vegh, Jens Verhaert, Jérôme Wahis, Eline Creemers, Lidia Yshii, Keimpe Wierda, Takashi Saito,[...]. EMBO Mol Med 2022
Marika Marino, Lujia Zhou, Melvin Y Rincon, Zsuzsanna Callaerts-Vegh, Jens Verhaert, Jérôme Wahis, Eline Creemers, Lidia Yshii, Keimpe Wierda, Takashi Saito,[...]. EMBO Mol Med 2022
AAV Vector-Mediated Antibody Delivery (A-MAD) in the Central Nervous System.
Marika Marino, Matthew G Holt. Front Neurol 2022
Marika Marino, Matthew G Holt. Front Neurol 2022
Characterization of Viral Genome Encapsidated in Adeno-associated Recombinant Vectors Produced in Yeast Saccharomyces cerevisiae.
Alvaro Galli, Ilenia Iaia, Maria Serena Milella, Filippo Cipriani, Veronica Della Latta, Mauro Giacca, Lorena Zentilin, Tiziana Cervelli. Mol Biotechnol 2021
Alvaro Galli, Ilenia Iaia, Maria Serena Milella, Filippo Cipriani, Veronica Della Latta, Mauro Giacca, Lorena Zentilin, Tiziana Cervelli. Mol Biotechnol 2021
MiniCAFE, a CRISPR/Cas9-based compact and potent transcriptional activator, elicits gene expression in vivo.
Xin Zhang, Sihan Lv, Zhenhuan Luo, Yongfei Hu, Xin Peng, Jie Lv, Shanshan Zhao, Jianqi Feng, Guanjie Huang, Qin-Li Wan,[...]. Nucleic Acids Res 2021
Xin Zhang, Sihan Lv, Zhenhuan Luo, Yongfei Hu, Xin Peng, Jie Lv, Shanshan Zhao, Jianqi Feng, Guanjie Huang, Qin-Li Wan,[...]. Nucleic Acids Res 2021
Advances and challenges in adeno-associated viral inner-ear gene therapy for sensorineural hearing loss.
Kamakshi Bankoti, Charles Generotti, Tiffany Hwa, Lili Wang, Bert W O'Malley, Daqing Li. Mol Ther Methods Clin Dev 2021
Kamakshi Bankoti, Charles Generotti, Tiffany Hwa, Lili Wang, Bert W O'Malley, Daqing Li. Mol Ther Methods Clin Dev 2021
Vectored Immunotherapeutics for Infectious Diseases: Can rAAVs Be The Game Changers for Fighting Transmissible Pathogens?
Wei Zhan, Manish Muhuri, Phillip W L Tai, Guangping Gao. Front Immunol 2021
Wei Zhan, Manish Muhuri, Phillip W L Tai, Guangping Gao. Front Immunol 2021
The Ocular Gene Delivery Landscape.
Bhubanananda Sahu, Isha Chug, Hemant Khanna. Biomolecules 2021
Bhubanananda Sahu, Isha Chug, Hemant Khanna. Biomolecules 2021